HRP20220652T1 - Pripravci i postupci unosa terapijskih sredstava - Google Patents

Pripravci i postupci unosa terapijskih sredstava Download PDF

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Publication number
HRP20220652T1
HRP20220652T1 HRP20220652TT HRP20220652T HRP20220652T1 HR P20220652 T1 HRP20220652 T1 HR P20220652T1 HR P20220652T T HRP20220652T T HR P20220652TT HR P20220652 T HRP20220652 T HR P20220652T HR P20220652 T1 HRP20220652 T1 HR P20220652T1
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HR
Croatia
Prior art keywords
lnp
lipid
mir
dose
peg
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HRP20220652TT
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English (en)
Croatian (hr)
Inventor
Gilles BESIN
Stephen Hoge
Joseph Senn
Kerry BENENATO
Staci SABNIS
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Modernatx, Inc.
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Publication date
Application filed by Modernatx, Inc. filed Critical Modernatx, Inc.
Publication of HRP20220652T1 publication Critical patent/HRP20220652T1/hr

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    • A61K48/0008—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition
    • A61K48/0025—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition wherein the non-active part clearly interacts with the delivered nucleic acid
    • A61K48/0033—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition wherein the non-active part clearly interacts with the delivered nucleic acid the non-active part being non-polymeric
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