PT3386484T - Composições e métodos para entrega de agentes terapêuticos - Google Patents

Composições e métodos para entrega de agentes terapêuticos

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Publication number
PT3386484T
PT3386484T PT168734895T PT16873489T PT3386484T PT 3386484 T PT3386484 T PT 3386484T PT 168734895 T PT168734895 T PT 168734895T PT 16873489 T PT16873489 T PT 16873489T PT 3386484 T PT3386484 T PT 3386484T
Authority
PT
Portugal
Prior art keywords
delivery
compositions
methods
therapeutic agents
therapeutic
Prior art date
Application number
PT168734895T
Other languages
English (en)
Original Assignee
Modernatx Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Modernatx Inc filed Critical Modernatx Inc
Publication of PT3386484T publication Critical patent/PT3386484T/pt

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    • A61K48/0008Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition
    • A61K48/0025Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition wherein the non-active part clearly interacts with the delivered nucleic acid
    • A61K48/0033Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition wherein the non-active part clearly interacts with the delivered nucleic acid the non-active part being non-polymeric
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