CN102256606A - 有效跳跃人杜兴肌营养不良基因外显子43、46、50-53中至少一个的方法和手段 - Google Patents
有效跳跃人杜兴肌营养不良基因外显子43、46、50-53中至少一个的方法和手段 Download PDFInfo
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- CN102256606A CN102256606A CN2009801519198A CN200980151919A CN102256606A CN 102256606 A CN102256606 A CN 102256606A CN 2009801519198 A CN2009801519198 A CN 2009801519198A CN 200980151919 A CN200980151919 A CN 200980151919A CN 102256606 A CN102256606 A CN 102256606A
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Abstract
Description
Claims (11)
Applications Claiming Priority (4)
Application Number | Priority Date | Filing Date | Title |
---|---|---|---|
EP07119351 | 2007-10-26 | ||
PCT/NL2008/050673 WO2009054725A2 (en) | 2007-10-26 | 2008-10-27 | Means and methods for counteracting muscle disorders |
NLPCT/NL2008/050673 | 2008-10-27 | ||
PCT/NL2009/050113 WO2010050802A2 (en) | 2008-10-27 | 2009-03-11 | Methods and means for efficient skipping of at least one of the following exons of the human duchenne muscular dystrophy gene: 43, 46, 50- 53. |
Related Child Applications (1)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
CN201510825064.XA Division CN105647921A (zh) | 2007-10-26 | 2009-03-11 | 有效跳跃人杜兴肌营养不良基因外显子43、46、50-53中至少一个的方法和手段 |
Publications (1)
Publication Number | Publication Date |
---|---|
CN102256606A true CN102256606A (zh) | 2011-11-23 |
Family
ID=39045623
Family Applications (5)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
CN200880120198XA Pending CN101896186A (zh) | 2007-10-26 | 2008-10-27 | 对抗肌肉病症的方式和方法 |
CN201610053552.8A Active CN105641700B (zh) | 2007-10-26 | 2008-10-27 | 对抗肌肉病症的方式和方法 |
CN200980152464.1A Active CN102264903B (zh) | 2007-10-26 | 2009-01-13 | 有效跳跃人杜兴肌营养不良前mRNA外显子45的方法和手段 |
CN2009801519198A Pending CN102256606A (zh) | 2007-10-26 | 2009-03-11 | 有效跳跃人杜兴肌营养不良基因外显子43、46、50-53中至少一个的方法和手段 |
CN201510825064.XA Pending CN105647921A (zh) | 2007-10-26 | 2009-03-11 | 有效跳跃人杜兴肌营养不良基因外显子43、46、50-53中至少一个的方法和手段 |
Family Applications Before (3)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
CN200880120198XA Pending CN101896186A (zh) | 2007-10-26 | 2008-10-27 | 对抗肌肉病症的方式和方法 |
CN201610053552.8A Active CN105641700B (zh) | 2007-10-26 | 2008-10-27 | 对抗肌肉病症的方式和方法 |
CN200980152464.1A Active CN102264903B (zh) | 2007-10-26 | 2009-01-13 | 有效跳跃人杜兴肌营养不良前mRNA外显子45的方法和手段 |
Family Applications After (1)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
CN201510825064.XA Pending CN105647921A (zh) | 2007-10-26 | 2009-03-11 | 有效跳跃人杜兴肌营养不良基因外显子43、46、50-53中至少一个的方法和手段 |
Country Status (17)
Country | Link |
---|---|
US (18) | US9243245B2 (zh) |
EP (4) | EP3238737B1 (zh) |
JP (6) | JP5600064B2 (zh) |
CN (5) | CN101896186A (zh) |
AU (1) | AU2008317566B2 (zh) |
CA (1) | CA2704049A1 (zh) |
CY (2) | CY1117286T1 (zh) |
DK (1) | DK2203173T3 (zh) |
ES (5) | ES2564563T3 (zh) |
HK (2) | HK1185098A1 (zh) |
HR (1) | HRP20160025T1 (zh) |
HU (2) | HUE028662T2 (zh) |
IL (4) | IL205322A (zh) |
NZ (2) | NZ584793A (zh) |
PL (1) | PL2203173T3 (zh) |
PT (1) | PT2203173E (zh) |
WO (1) | WO2009054725A2 (zh) |
Cited By (4)
Publication number | Priority date | Publication date | Assignee | Title |
---|---|---|---|---|
CN105307723A (zh) * | 2013-03-15 | 2016-02-03 | 萨勒普塔医疗公司 | 改进的用于治疗肌营养不良的组合物 |
CN106714845A (zh) * | 2014-08-11 | 2017-05-24 | 得克萨斯州大学系统董事会 | 通过crispr/cas9介导的基因编辑预防肌营养不良 |
CN107667174A (zh) * | 2015-05-21 | 2018-02-06 | ProQR治疗上市公司Ⅱ | 治疗营养不良型大疱性表皮松解症的反义寡核苷酸 |
CN110257379A (zh) * | 2012-07-03 | 2019-09-20 | 马林生物科技有限公司 | 用于治疗肌肉萎缩症患者的寡核苷酸 |
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CN106714845A (zh) * | 2014-08-11 | 2017-05-24 | 得克萨斯州大学系统董事会 | 通过crispr/cas9介导的基因编辑预防肌营养不良 |
CN107667174A (zh) * | 2015-05-21 | 2018-02-06 | ProQR治疗上市公司Ⅱ | 治疗营养不良型大疱性表皮松解症的反义寡核苷酸 |
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