BR122020016865B1 - Oligonucleotídeo antisenso, composição farmacêutica compreendendo o mesmo e uso da dita composição para o tratamento de distrofia muscular de duchenne (dmd) - Google Patents

Oligonucleotídeo antisenso, composição farmacêutica compreendendo o mesmo e uso da dita composição para o tratamento de distrofia muscular de duchenne (dmd) Download PDF

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Publication number
BR122020016865B1
BR122020016865B1 BR122020016865-0A BR122020016865A BR122020016865B1 BR 122020016865 B1 BR122020016865 B1 BR 122020016865B1 BR 122020016865 A BR122020016865 A BR 122020016865A BR 122020016865 B1 BR122020016865 B1 BR 122020016865B1
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antisense
dystrophin
seq
oligomer
exon
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BR122020016865-0A
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English (en)
Portuguese (pt)
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Richard K. Bestwick
Diane Elizabeth Frank
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Sarepta Therapeutics, Inc.
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BR122020016865-0A 2013-03-14 2014-03-14 Oligonucleotídeo antisenso, composição farmacêutica compreendendo o mesmo e uso da dita composição para o tratamento de distrofia muscular de duchenne (dmd) BR122020016865B1 (pt)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201361784547P 2013-03-14 2013-03-14
US61/784.547 2013-03-14
PCT/US2014/029689 WO2014153220A2 (en) 2013-03-14 2014-03-14 Exon skipping compositions for treating muscular dystrophy

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BR122020016865B1 true BR122020016865B1 (pt) 2022-12-27

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BR122020016865-0A BR122020016865B1 (pt) 2013-03-14 2014-03-14 Oligonucleotídeo antisenso, composição farmacêutica compreendendo o mesmo e uso da dita composição para o tratamento de distrofia muscular de duchenne (dmd)
BR112015023001A BR112015023001B8 (pt) 2013-03-14 2014-03-14 Oligonucleotídeo antisenso, composição farmacêutica compreendendo o mesmo e uso da dita composição para o tratamento de distrofia muscular de duchenne (dmd)

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US (11) US9217148B2 (enExample)
EP (3) EP3633035A1 (enExample)
JP (5) JP6449231B2 (enExample)
KR (7) KR102521608B1 (enExample)
CN (3) CN117844807A (enExample)
AU (4) AU2014236140B2 (enExample)
BR (2) BR122020016865B1 (enExample)
CA (1) CA2906209A1 (enExample)
EA (2) EA202090946A3 (enExample)
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IL (3) IL293975B1 (enExample)
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