EA202090946A2 - Композиции, обеспечивающие пропускание экзонов, для лечения мышечной дистрофии - Google Patents

Композиции, обеспечивающие пропускание экзонов, для лечения мышечной дистрофии

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Publication number
EA202090946A2
EA202090946A2 EA202090946A EA202090946A EA202090946A2 EA 202090946 A2 EA202090946 A2 EA 202090946A2 EA 202090946 A EA202090946 A EA 202090946A EA 202090946 A EA202090946 A EA 202090946A EA 202090946 A2 EA202090946 A2 EA 202090946A2
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EA
Eurasian Patent Office
Prior art keywords
exone
leaking
treatment
compositions providing
muscle dystrophy
Prior art date
Application number
EA202090946A
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English (en)
Other versions
EA202090946A3 (ru
Inventor
Ричард К. Бестуик
Дайан Элизабет Франк
Фред Джозеф Шнелль
Original Assignee
Сарепта Терапьютикс, Инк.
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Application filed by Сарепта Терапьютикс, Инк. filed Critical Сарепта Терапьютикс, Инк.
Publication of EA202090946A2 publication Critical patent/EA202090946A2/ru
Publication of EA202090946A3 publication Critical patent/EA202090946A3/ru

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Abstract

Описаны антисмысловые молекулы, способные связываться с выбранным участком-мишенью в гене дистрофина человека, для индукции пропускания экзона 44.
EA202090946A 2013-03-14 2014-03-14 Композиции, обеспечивающие пропускание экзонов, для лечения мышечной дистрофии EA202090946A3 (ru)

Applications Claiming Priority (1)

Application Number Priority Date Filing Date Title
US201361784547P 2013-03-14 2013-03-14

Publications (2)

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EA202090946A2 true EA202090946A2 (ru) 2021-04-30
EA202090946A3 EA202090946A3 (ru) 2021-07-30

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ID=50694004

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Application Number Title Priority Date Filing Date
EA202090946A EA202090946A3 (ru) 2013-03-14 2014-03-14 Композиции, обеспечивающие пропускание экзонов, для лечения мышечной дистрофии
EA201591767A EA035882B1 (ru) 2013-03-14 2014-03-14 Антисмысловые олигонуклеотиды, обеспечивающие пропуск экзонов, для лечения мышечной дистрофии

Family Applications After (1)

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EA201591767A EA035882B1 (ru) 2013-03-14 2014-03-14 Антисмысловые олигонуклеотиды, обеспечивающие пропуск экзонов, для лечения мышечной дистрофии

Country Status (16)

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US (9) US9217148B2 (ru)
EP (3) EP3998339A1 (ru)
JP (5) JP6449231B2 (ru)
KR (6) KR20230116945A (ru)
CN (3) CN110218727A (ru)
AU (3) AU2014236140B2 (ru)
BR (2) BR122020016865B1 (ru)
CA (1) CA2906209A1 (ru)
EA (2) EA202090946A3 (ru)
ES (1) ES2762881T3 (ru)
HK (1) HK1219755A1 (ru)
IL (3) IL280443B (ru)
MX (2) MX366485B (ru)
NZ (4) NZ775701A (ru)
SA (1) SA515361125B1 (ru)
WO (1) WO2014153220A2 (ru)

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