JP6868617B2 - 低ホスファターゼ血症の組織非特異的アルカリホスファターゼ(tnsalp)酵素補充療法に有効な投薬計画の特定 - Google Patents

低ホスファターゼ血症の組織非特異的アルカリホスファターゼ(tnsalp)酵素補充療法に有効な投薬計画の特定 Download PDF

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JP6868617B2
JP6868617B2 JP2018515934A JP2018515934A JP6868617B2 JP 6868617 B2 JP6868617 B2 JP 6868617B2 JP 2018515934 A JP2018515934 A JP 2018515934A JP 2018515934 A JP2018515934 A JP 2018515934A JP 6868617 B2 JP6868617 B2 JP 6868617B2
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プラッドハン,ラジェンドラ
ガオ,シアン
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アレクシオン ファーマシューティカルズ, インコーポレイテッド
アレクシオン ファーマシューティカルズ, インコーポレイテッド
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    • C12Y301/00Hydrolases acting on ester bonds (3.1)
    • C12Y301/03Phosphoric monoester hydrolases (3.1.3)
    • C12Y301/03001Alkaline phosphatase (3.1.3.1)
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    • G01N2800/52Predicting or monitoring the response to treatment, e.g. for selection of therapy based on assay results in personalised medicine; Prognosis

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JP2018515934A 2015-09-28 2016-09-27 低ホスファターゼ血症の組織非特異的アルカリホスファターゼ(tnsalp)酵素補充療法に有効な投薬計画の特定 Active JP6868617B2 (ja)

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US201562234025P 2015-09-28 2015-09-28
US62/234,025 2015-09-28
US201562238015P 2015-10-06 2015-10-06
US62/238,015 2015-10-06
PCT/US2016/054013 WO2017058822A1 (en) 2015-09-28 2016-09-27 Identifying effective dosage regimens for tissue non-specific alkaline phosphatase (tnsalp)-enzyme replacement therapy of hypophosphatasia

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JP2018528252A JP2018528252A (ja) 2018-09-27
JP2018528252A5 JP2018528252A5 (cg-RX-API-DMAC7.html) 2019-10-03
JP6868617B2 true JP6868617B2 (ja) 2021-05-12

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