JP6667453B2 - 成長ホルモン受容体発現を調節するための組成物及び方法 - Google Patents

成長ホルモン受容体発現を調節するための組成物及び方法 Download PDF

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JP6667453B2
JP6667453B2 JP2016565461A JP2016565461A JP6667453B2 JP 6667453 B2 JP6667453 B2 JP 6667453B2 JP 2016565461 A JP2016565461 A JP 2016565461A JP 2016565461 A JP2016565461 A JP 2016565461A JP 6667453 B2 JP6667453 B2 JP 6667453B2
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certain embodiments
oligonucleotide
antisense
compound
nucleic acid
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JP2017518278A (ja
JP2017518278A5 (enExample
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プラカシュ，タジャ・ピー
セス，プニット・ピー
スウェイジ，エリック・イー
バーノット，サンジェイ
フレアー，スーザン・エム
ブイ，フィン・ホア
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Ionis Pharmaceuticals Inc
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Ionis Pharmaceuticals Inc
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JP2016565461A 2014-05-01 2015-05-01 成長ホルモン受容体発現を調節するための組成物及び方法 Expired - Fee Related JP6667453B2 (ja)

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US201461987470P 2014-05-01 2014-05-01
US61/987,470 2014-05-01
US201462061071P 2014-10-07 2014-10-07
US62/061,071 2014-10-07
US201462082511P 2014-11-20 2014-11-20
US62/082,511 2014-11-20
PCT/US2015/028887 WO2015168618A2 (en) 2014-05-01 2015-05-01 Compositions and methods for modulating growth hormone receptor expression

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JP6667453B2 (ja) 2014-05-01 2020-03-18 アイオーニス ファーマシューティカルズ， インコーポレーテッドＩｏｎｉｓ Ｐｈａｒｍａｃｅｕｔｉｃａｌｓ，Ｉｎｃ． 成長ホルモン受容体発現を調節するための組成物及び方法
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WO2019126641A2 (en) * 2017-12-21 2019-06-27 Ionis Pharmaceuticals, Inc. Modulation of frataxin expression
EP4025252A4 (en) 2019-09-03 2023-10-18 Arcturus Therapeutics, Inc. ASIALOGLYCOPROTEIN RECEPTOR-MEDIATED ADMINISTRATION OF THERAPEUTICALLY ACTIVE CONJUGATES
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CA3226651A1 (en) * 2021-08-03 2023-02-09 Kallanthottathil G. Rajeev Compositions and methods for targeted rna delivery
US11692001B2 (en) 2021-08-30 2023-07-04 Hongene Biotech Corporation Functionalized n-acetylgalactosamine analogs
EP4448540A1 (en) 2021-12-15 2024-10-23 Hongene Biotech Corporation Functionalized n-acetylgalactosamine analogs
WO2024001172A1 (en) * 2022-06-27 2024-01-04 Ractigen Therapeutics Oligonucleotide modulators activating complement factor h expression
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