JP2019501892A5 - - Google Patents

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JP2019501892A5
JP2019501892A5 JP2018529250A JP2018529250A JP2019501892A5 JP 2019501892 A5 JP2019501892 A5 JP 2019501892A5 JP 2018529250 A JP2018529250 A JP 2018529250A JP 2018529250 A JP2018529250 A JP 2018529250A JP 2019501892 A5 JP2019501892 A5 JP 2019501892A5
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mrna
retained intron
pharmaceutical composition
ric pre
protein
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JP2018529250A
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JP2019501892A (ja
JP7049248B2 (ja
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Priority claimed from PCT/US2016/066708 external-priority patent/WO2017106377A1/en
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Priority to JP2022013860A priority Critical patent/JP2022062140A/ja
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JP2018529250A 2015-12-14 2016-12-14 常染色体優性精神遅滞-5とドラベ症候群の処置のためのアンチセンスオリゴマー Expired - Fee Related JP7049248B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2022013860A JP2022062140A (ja) 2015-12-14 2022-02-01 常染色体優性精神遅滞-5とドラベ症候群の処置のためのアンチセンスオリゴマー

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201562267251P 2015-12-14 2015-12-14
US62/267,251 2015-12-14
PCT/US2016/066708 WO2017106377A1 (en) 2015-12-14 2016-12-14 Antisense oligomers for treatment of autosomal dominant mental retardation-5 and dravet syndrome

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JP2022013860A Division JP2022062140A (ja) 2015-12-14 2022-02-01 常染色体優性精神遅滞-5とドラベ症候群の処置のためのアンチセンスオリゴマー

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JP2019501892A JP2019501892A (ja) 2019-01-24
JP2019501892A5 true JP2019501892A5 (enExample) 2020-01-30
JP7049248B2 JP7049248B2 (ja) 2022-04-06

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JP2018529250A Expired - Fee Related JP7049248B2 (ja) 2015-12-14 2016-12-14 常染色体優性精神遅滞-5とドラベ症候群の処置のためのアンチセンスオリゴマー
JP2022013860A Pending JP2022062140A (ja) 2015-12-14 2022-02-01 常染色体優性精神遅滞-5とドラベ症候群の処置のためのアンチセンスオリゴマー

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Country Status (11)

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US (2) US11083745B2 (enExample)
EP (2) EP3933041B1 (enExample)
JP (2) JP7049248B2 (enExample)
KR (1) KR102604132B1 (enExample)
CN (2) CN109312343B (enExample)
AU (2) AU2016370653A1 (enExample)
CA (1) CA3005256A1 (enExample)
ES (1) ES2882500T3 (enExample)
IL (1) IL259222A (enExample)
SG (1) SG11201804443UA (enExample)
WO (1) WO2017106377A1 (enExample)

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