JP2019500349A5 - - Google Patents

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Publication number
JP2019500349A5
JP2019500349A5 JP2018529257A JP2018529257A JP2019500349A5 JP 2019500349 A5 JP2019500349 A5 JP 2019500349A5 JP 2018529257 A JP2018529257 A JP 2018529257A JP 2018529257 A JP2018529257 A JP 2018529257A JP 2019500349 A5 JP2019500349 A5 JP 2019500349A5
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JP
Japan
Prior art keywords
protein
stxbp1
mrna
pharmaceutical composition
composition according
Prior art date
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JP2018529257A
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English (en)
Japanese (ja)
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JP2019500349A (ja
JP7049249B2 (ja
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Priority claimed from PCT/US2016/066721 external-priority patent/WO2017106382A1/en
Publication of JP2019500349A publication Critical patent/JP2019500349A/ja
Publication of JP2019500349A5 publication Critical patent/JP2019500349A5/ja
Priority to JP2022013867A priority Critical patent/JP2022062141A/ja
Application granted granted Critical
Publication of JP7049249B2 publication Critical patent/JP7049249B2/ja
Expired - Fee Related legal-status Critical Current
Anticipated expiration legal-status Critical

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JP2018529257A 2015-12-14 2016-12-14 中枢神経系疾患の処置のための組成物および方法 Expired - Fee Related JP7049249B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2022013867A JP2022062141A (ja) 2015-12-14 2022-02-01 中枢神経系疾患の処置のための組成物および方法

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201562267256P 2015-12-14 2015-12-14
US62/267,256 2015-12-14
US201662319011P 2016-04-06 2016-04-06
US62/319,011 2016-04-06
PCT/US2016/066721 WO2017106382A1 (en) 2015-12-14 2016-12-14 Compositions and methods for treatment of central nervous system diseases

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2022013867A Division JP2022062141A (ja) 2015-12-14 2022-02-01 中枢神経系疾患の処置のための組成物および方法

Publications (3)

Publication Number Publication Date
JP2019500349A JP2019500349A (ja) 2019-01-10
JP2019500349A5 true JP2019500349A5 (enExample) 2020-01-30
JP7049249B2 JP7049249B2 (ja) 2022-04-06

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JP2018529257A Expired - Fee Related JP7049249B2 (ja) 2015-12-14 2016-12-14 中枢神経系疾患の処置のための組成物および方法
JP2022013867A Pending JP2022062141A (ja) 2015-12-14 2022-02-01 中枢神経系疾患の処置のための組成物および方法

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JP2022013867A Pending JP2022062141A (ja) 2015-12-14 2022-02-01 中枢神経系疾患の処置のための組成物および方法

Country Status (4)

Country Link
EP (2) EP3389725B1 (enExample)
JP (2) JP7049249B2 (enExample)
CA (1) CA3005246A1 (enExample)
WO (1) WO2017106382A1 (enExample)

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CA3162618A1 (en) 2019-03-20 2020-09-24 Peter Jungsoo PARK Antisense oligonucleotide-based progranulin augmentation therapy in neurodegenerative diseases
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US12338437B2 (en) 2020-05-11 2025-06-24 Stoke Therapeutics, Inc. OPA1 antisense oligomers for treatment of conditions and diseases
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WO2023143425A1 (zh) * 2022-01-25 2023-08-03 上海魁特迪生物科技有限公司 改善认知障碍的方法
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CN114836532A (zh) * 2022-04-28 2022-08-02 福建医科大学附属第一医院 Eif2b5基因突变作为靶标在诊断消融性白质脑病中的应用
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