JP2018538287A5 - - Google Patents
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- Publication number
- JP2018538287A5 JP2018538287A5 JP2018529219A JP2018529219A JP2018538287A5 JP 2018538287 A5 JP2018538287 A5 JP 2018538287A5 JP 2018529219 A JP2018529219 A JP 2018529219A JP 2018529219 A JP2018529219 A JP 2018529219A JP 2018538287 A5 JP2018538287 A5 JP 2018538287A5
- Authority
- JP
- Japan
- Prior art keywords
- mrna
- protein
- item
- pharmaceutical composition
- composition according
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Withdrawn
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2022000102A JP2022046723A (ja) | 2015-12-14 | 2022-01-04 | 多発性嚢胞腎の処置のためのアンチセンスオリゴマー |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201562267252P | 2015-12-14 | 2015-12-14 | |
| US62/267,252 | 2015-12-14 | ||
| PCT/US2016/066417 WO2017106211A1 (en) | 2015-12-14 | 2016-12-13 | Antisense oligomers for treatment of polycystic kidney disease |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022000102A Division JP2022046723A (ja) | 2015-12-14 | 2022-01-04 | 多発性嚢胞腎の処置のためのアンチセンスオリゴマー |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2018538287A JP2018538287A (ja) | 2018-12-27 |
| JP2018538287A5 true JP2018538287A5 (enExample) | 2020-01-30 |
Family
ID=59057523
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2018529219A Withdrawn JP2018538287A (ja) | 2015-12-14 | 2016-12-13 | 多発性嚢胞腎の処置のためのアンチセンスオリゴマー |
| JP2022000102A Pending JP2022046723A (ja) | 2015-12-14 | 2022-01-04 | 多発性嚢胞腎の処置のためのアンチセンスオリゴマー |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022000102A Pending JP2022046723A (ja) | 2015-12-14 | 2022-01-04 | 多発性嚢胞腎の処置のためのアンチセンスオリゴマー |
Country Status (4)
| Country | Link |
|---|---|
| EP (1) | EP3389782A4 (enExample) |
| JP (2) | JP2018538287A (enExample) |
| CA (1) | CA3005247A1 (enExample) |
| WO (1) | WO2017106211A1 (enExample) |
Families Citing this family (12)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| GB201410693D0 (en) | 2014-06-16 | 2014-07-30 | Univ Southampton | Splicing modulation |
| CN107109411B (zh) | 2014-10-03 | 2022-07-01 | 冷泉港实验室 | 核基因输出的定向增加 |
| CN108603230A (zh) | 2015-10-09 | 2018-09-28 | 南安普敦大学 | 基因表达的调节与蛋白质表达失调的筛选 |
| US11096956B2 (en) | 2015-12-14 | 2021-08-24 | Stoke Therapeutics, Inc. | Antisense oligomers and uses thereof |
| CN116059236A (zh) | 2015-12-14 | 2023-05-05 | 冷泉港实验室 | 用于治疗常染色体显性精神发育迟滞5型和Dravet综合征的反义寡聚体 |
| KR20260009385A (ko) | 2017-08-25 | 2026-01-19 | 스톡 테라퓨틱스, 인크. | 병태 및 질환 치료용 안티센스 올리고머 |
| JP2021523227A (ja) | 2018-05-04 | 2021-09-02 | ストーク セラピューティクス，インク． | コレステリルエステル蓄積症の処置のための方法及び組成物 |
| KR20210134003A (ko) | 2019-02-27 | 2021-11-08 | 스톡 테라퓨틱스, 인크. | 병태 및 질환의 치료를 위한 안티센스 올리고머 |
| KR20220104677A (ko) * | 2019-08-19 | 2022-07-26 | 스톡 테라퓨틱스, 인크. | 스플라이싱 및 단백질 발현을 조절하기 위한 조성물 및 방법 |
| US12338437B2 (en) | 2020-05-11 | 2025-06-24 | Stoke Therapeutics, Inc. | OPA1 antisense oligomers for treatment of conditions and diseases |
| CA3207341A1 (en) * | 2021-02-03 | 2022-08-11 | Isabel AZNAREZ | Compositions for treatment of conditions and diseases associated with polycystin expression |
| WO2024254639A1 (en) * | 2023-06-16 | 2024-12-19 | PYC Therapeutics Limited | Compositions and methods for treatment of kidney disease |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20040102402A1 (en) * | 2002-11-22 | 2004-05-27 | Isis Pharmaceuticals Inc. | Modulation of tissue factor expression |
| US8007790B2 (en) * | 2006-04-03 | 2011-08-30 | Stowers Institute For Medical Research | Methods for treating polycystic kidney disease (PKD) or other cyst forming diseases |
| CA2993381C (en) * | 2006-07-24 | 2020-07-14 | Athena Diagnostics, Inc. | Method of detecting the occurrence of adpkd based on presence of nucleotide sequence alteration in pkd1 |
| WO2013173637A1 (en) * | 2012-05-16 | 2013-11-21 | Rana Therapeutics, Inc. | Compositions and methods for modulating gene expression |
| WO2015035091A1 (en) * | 2013-09-04 | 2015-03-12 | Cold Spring Harbor Laboratory | Reducing nonsense-mediated mrna decay |
| CN107109411B (zh) * | 2014-10-03 | 2022-07-01 | 冷泉港实验室 | 核基因输出的定向增加 |
-
2016
- 2016-12-13 CA CA3005247A patent/CA3005247A1/en active Pending
- 2016-12-13 JP JP2018529219A patent/JP2018538287A/ja not_active Withdrawn
- 2016-12-13 EP EP16876500.6A patent/EP3389782A4/en not_active Withdrawn
- 2016-12-13 WO PCT/US2016/066417 patent/WO2017106211A1/en not_active Ceased
-
2022
- 2022-01-04 JP JP2022000102A patent/JP2022046723A/ja active Pending
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