JP2017513469A5 - - Google Patents

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JP2017513469A5
JP2017513469A5 JP2016560543A JP2016560543A JP2017513469A5 JP 2017513469 A5 JP2017513469 A5 JP 2017513469A5 JP 2016560543 A JP2016560543 A JP 2016560543A JP 2016560543 A JP2016560543 A JP 2016560543A JP 2017513469 A5 JP2017513469 A5 JP 2017513469A5
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modified
tds
sugar
internucleoside linkage
compound
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JP2016560543A
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JP2017513469A (ja
JP6622214B2 (ja
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Priority claimed from PCT/US2015/023934 external-priority patent/WO2015153800A2/en
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JP2016560543A 2014-04-01 2015-04-01 Sod−1発現を調節するための組成物 Active JP6622214B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201461973803P 2014-04-01 2014-04-01
US61/973,803 2014-04-01
PCT/US2015/023934 WO2015153800A2 (en) 2014-04-01 2015-04-01 Compositions for modulating sod-1 expression

Related Child Applications (1)

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JP2019141933A Division JP2019201664A (ja) 2014-04-01 2019-08-01 Sod−1発現を調節するための組成物

Publications (3)

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JP2017513469A JP2017513469A (ja) 2017-06-01
JP2017513469A5 true JP2017513469A5 (enExample) 2018-06-14
JP6622214B2 JP6622214B2 (ja) 2019-12-18

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JP2016560543A Active JP6622214B2 (ja) 2014-04-01 2015-04-01 Sod−1発現を調節するための組成物
JP2019141933A Withdrawn JP2019201664A (ja) 2014-04-01 2019-08-01 Sod−1発現を調節するための組成物
JP2021014429A Active JP7198298B2 (ja) 2014-04-01 2021-02-01 Sod-1発現を調節するための組成物
JP2022200959A Withdrawn JP2023027299A (ja) 2014-04-01 2022-12-16 Sod-1発現を調節するための組成物
JP2024085318A Pending JP2024105714A (ja) 2014-04-01 2024-05-27 Sod-1発現を調節するための組成物
JP2025210099A Pending JP2026035746A (ja) 2014-04-01 2025-12-01 Sod-1発現を調節するための組成物

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JP2019141933A Withdrawn JP2019201664A (ja) 2014-04-01 2019-08-01 Sod−1発現を調節するための組成物
JP2021014429A Active JP7198298B2 (ja) 2014-04-01 2021-02-01 Sod-1発現を調節するための組成物
JP2022200959A Withdrawn JP2023027299A (ja) 2014-04-01 2022-12-16 Sod-1発現を調節するための組成物
JP2024085318A Pending JP2024105714A (ja) 2014-04-01 2024-05-27 Sod-1発現を調節するための組成物
JP2025210099A Pending JP2026035746A (ja) 2014-04-01 2025-12-01 Sod-1発現を調節するための組成物

Country Status (31)

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US (3) US10385341B2 (enExample)
EP (3) EP3126499B1 (enExample)
JP (6) JP6622214B2 (enExample)
KR (6) KR20210097225A (enExample)
CN (2) CN106459972B (enExample)
AU (4) AU2015240761B2 (enExample)
BR (1) BR112016021848B1 (enExample)
CA (2) CA3250848A1 (enExample)
CL (3) CL2016002509A1 (enExample)
CY (3) CY1123288T1 (enExample)
DK (2) DK3126499T3 (enExample)
ES (2) ES2926869T3 (enExample)
FI (1) FIC20240035I1 (enExample)
FR (1) FR24C1039I2 (enExample)
HR (2) HRP20220798T1 (enExample)
HU (3) HUE050704T2 (enExample)
IL (2) IL247714B (enExample)
LT (3) LT3757214T (enExample)
LU (1) LUC00359I2 (enExample)
MX (2) MX373908B (enExample)
MY (2) MY175665A (enExample)
NL (1) NL301293I2 (enExample)
NZ (1) NZ724100A (enExample)
PL (2) PL3757214T3 (enExample)
PT (2) PT3126499T (enExample)
RS (2) RS60707B1 (enExample)
RU (1) RU2704619C2 (enExample)
SG (3) SG10201906520RA (enExample)
SI (2) SI3126499T1 (enExample)
SM (2) SMT202000456T1 (enExample)
WO (1) WO2015153800A2 (enExample)

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TWI906204B (zh) * 2018-12-14 2025-12-01 美商百健Ma公司 用於治療及預防肌肉萎縮性脊髓側索硬化症之組合物及方法
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JP2022520885A (ja) * 2019-03-26 2022-04-01 ラトガース,ザ ステート ユニバーシティ オブ ニュー ジャージー 神経変性疾患を処置するための組成物および方法
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CN114206897B (zh) 2019-05-08 2024-09-20 比奥根Ma公司 寡核苷酸的汇聚液相合成
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JP2024513403A (ja) 2021-04-01 2024-03-25 バイオジェン・エムエイ・インコーポレイテッド 中枢神経系への核酸送達
WO2023081908A2 (en) * 2021-11-08 2023-05-11 University Of Massachusetts Oligonucleotides for sod1 modulation
CN114369130B (zh) * 2021-12-28 2023-10-03 杭州天龙药业有限公司 修饰的硫代寡核苷酸及其应用
JP2025522433A (ja) 2022-06-15 2025-07-15 アローヘッド ファーマシューティカルズ インコーポレイテッド スーパーオキシドジスムターゼ1(SOD1)の発現を阻害するためのRNAi剤、その組成物、及び使用の方法
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