KR102709597B1 - 리소좀 장애를 위한 유전자 요법 - Google Patents

리소좀 장애를 위한 유전자 요법 Download PDF

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KR102709597B1
KR102709597B1 KR1020227002136A KR20227002136A KR102709597B1 KR 102709597 B1 KR102709597 B1 KR 102709597B1 KR 1020227002136 A KR1020227002136 A KR 1020227002136A KR 20227002136 A KR20227002136 A KR 20227002136A KR 102709597 B1 KR102709597 B1 KR 102709597B1
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nucleic acid
raav
vector
sequence
itr
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KR20220015500A (ko
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아사 아벨리오비치
로라 헤크만
허브 린
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프리베일 테라퓨틱스, 인크.
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KR1020227002136A 2017-10-03 2018-10-03 리소좀 장애를 위한 유전자 요법 Active KR102709597B1 (ko)

Applications Claiming Priority (12)

Application Number Priority Date Filing Date Title
US201762567301P 2017-10-03 2017-10-03
US201762567296P 2017-10-03 2017-10-03
US201762567310P 2017-10-03 2017-10-03
US201762567319P 2017-10-03 2017-10-03
US201762567311P 2017-10-03 2017-10-03
US62/567,310 2017-10-03
US62/567,296 2017-10-03
US62/567,311 2017-10-03
US62/567,301 2017-10-03
US62/567,319 2017-10-03
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