MX2020003965A - Terapias genicas para los trastornos lisosomales. - Google Patents

Terapias genicas para los trastornos lisosomales.

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Publication number
MX2020003965A
MX2020003965A MX2020003965A MX2020003965A MX2020003965A MX 2020003965 A MX2020003965 A MX 2020003965A MX 2020003965 A MX2020003965 A MX 2020003965A MX 2020003965 A MX2020003965 A MX 2020003965A MX 2020003965 A MX2020003965 A MX 2020003965A
Authority
MX
Mexico
Prior art keywords
disease
gene therapies
lysosomal disorders
expression constructs
disclosure provides
Prior art date
Application number
MX2020003965A
Other languages
English (en)
Spanish (es)
Inventor
Asa Abeliovich
Laura Heckman
Herve Rhinn
Original Assignee
Prevail Therapeutics Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Prevail Therapeutics Inc filed Critical Prevail Therapeutics Inc
Publication of MX2020003965A publication Critical patent/MX2020003965A/es

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    • C12N9/14—Hydrolases (3)
    • C12N9/24—Hydrolases (3) acting on glycosyl compounds (3.2)
    • C12N9/2402—Hydrolases (3) acting on glycosyl compounds (3.2) hydrolysing O- and S- glycosyl compounds (3.2.1)
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    • A61K48/005—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'active' part of the composition delivered, i.e. the nucleic acid delivered
    • A61K48/0058—Nucleic acids adapted for tissue specific expression, e.g. having tissue specific promoters as part of a contruct
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MX2020003965A 2017-10-03 2018-10-03 Terapias genicas para los trastornos lisosomales. MX2020003965A (es)

Applications Claiming Priority (6)

Application Number Priority Date Filing Date Title
US201762567310P 2017-10-03 2017-10-03
US201762567319P 2017-10-03 2017-10-03
US201762567296P 2017-10-03 2017-10-03
US201762567301P 2017-10-03 2017-10-03
US201762567311P 2017-10-03 2017-10-03
PCT/US2018/054227 WO2019070894A1 (en) 2017-10-03 2018-10-03 GENE THERAPIES FOR LYSOSOMIAL DISORDERS

Publications (1)

Publication Number Publication Date
MX2020003965A true MX2020003965A (es) 2020-10-05

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MX2020003965A MX2020003965A (es) 2017-10-03 2018-10-03 Terapias genicas para los trastornos lisosomales.
MX2020011747A MX2020011747A (es) 2017-10-03 2020-07-13 Terapias genicas para los trastornos lisosomales.
MX2020011746A MX2020011746A (es) 2017-10-03 2020-07-13 Terapias genicas para los trastornos lisosomales.

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