KR102008708B1 - 전압 작동 나트륨 통로, 알파 소단위(scna)에 대한 자연 안티센스 전사체의 저해에 의한 전압 작동 나트륨 통로, 알파 소단위(scna) 관련된 질환의 치료 - Google Patents

전압 작동 나트륨 통로, 알파 소단위(scna)에 대한 자연 안티센스 전사체의 저해에 의한 전압 작동 나트륨 통로, 알파 소단위(scna) 관련된 질환의 치료 Download PDF

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KR102008708B1
KR102008708B1 KR1020187027848A KR20187027848A KR102008708B1 KR 102008708 B1 KR102008708 B1 KR 102008708B1 KR 1020187027848 A KR1020187027848 A KR 1020187027848A KR 20187027848 A KR20187027848 A KR 20187027848A KR 102008708 B1 KR102008708 B1 KR 102008708B1
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antisense
oligonucleotides
oligonucleotide
rna
scn1a
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조셉 콜라드
올가 크로코바 셔만
벨린다 데 레온
카를로스 코이토
제인 에이치. 디알. 하시아오
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큐알엔에이, 인크.
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KR1020187027848A 2010-06-23 2011-06-23 전압 작동 나트륨 통로, 알파 소단위(scna)에 대한 자연 안티센스 전사체의 저해에 의한 전압 작동 나트륨 통로, 알파 소단위(scna) 관련된 질환의 치료 Active KR102008708B1 (ko)

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US35777410P 2010-06-23 2010-06-23
US61/357,774 2010-06-23
PCT/US2011/041664 WO2011163499A2 (en) 2010-06-23 2011-06-23 Treatment of sodium channel, voltage-gated, alpha subunit (scna) related diseases by inhibition of natural antisense transcript to scna

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KR1020137001746A Division KR101914309B1 (ko) 2010-06-23 2011-06-23 전압 작동 나트륨 통로, 알파 소단위(scna)에 대한 자연 안티센스 전사체의 저해에 의한 전압 작동 나트륨 통로, 알파 소단위(scna) 관련된 질환의 치료

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KR1020197022794A Division KR102152931B1 (ko) 2010-06-23 2011-06-23 전압 작동 나트륨 통로, 알파 소단위(scna)에 대한 자연 안티센스 전사체의 저해에 의한 전압 작동 나트륨 통로, 알파 소단위(scna) 관련된 질환의 치료

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KR20180110195A KR20180110195A (ko) 2018-10-08
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KR1020187027848A Active KR102008708B1 (ko) 2010-06-23 2011-06-23 전압 작동 나트륨 통로, 알파 소단위(scna)에 대한 자연 안티센스 전사체의 저해에 의한 전압 작동 나트륨 통로, 알파 소단위(scna) 관련된 질환의 치료
KR1020197022794A Active KR102152931B1 (ko) 2010-06-23 2011-06-23 전압 작동 나트륨 통로, 알파 소단위(scna)에 대한 자연 안티센스 전사체의 저해에 의한 전압 작동 나트륨 통로, 알파 소단위(scna) 관련된 질환의 치료
KR1020137001746A Active KR101914309B1 (ko) 2010-06-23 2011-06-23 전압 작동 나트륨 통로, 알파 소단위(scna)에 대한 자연 안티센스 전사체의 저해에 의한 전압 작동 나트륨 통로, 알파 소단위(scna) 관련된 질환의 치료

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KR1020137001746A Active KR101914309B1 (ko) 2010-06-23 2011-06-23 전압 작동 나트륨 통로, 알파 소단위(scna)에 대한 자연 안티센스 전사체의 저해에 의한 전압 작동 나트륨 통로, 알파 소단위(scna) 관련된 질환의 치료

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CA2817256A1 (en) 2010-11-12 2012-05-18 The General Hospital Corporation Polycomb-associated non-coding rnas
US9920317B2 (en) 2010-11-12 2018-03-20 The General Hospital Corporation Polycomb-associated non-coding RNAs
CA3077910A1 (en) 2010-11-17 2012-05-24 Ionis Pharmaceuticals, Inc. Modulation of alpha synuclein expression
JP6125505B2 (ja) * 2011-09-06 2017-05-10 カッパーアールエヌエー，インコーポレイテッド 小分子による電位開口型ナトリウムチャネル・アルファサブユニット関連疾患の治療
US20150152410A1 (en) 2012-05-16 2015-06-04 Rana Therapeutics, Inc. Compositions and methods for modulating mecp2 expression
AU2013262700A1 (en) 2012-05-16 2015-01-22 Rana Therapeutics, Inc. Compositions and methods for modulating hemoglobin gene family expression
WO2013173598A1 (en) 2012-05-16 2013-11-21 Rana Therapeutics, Inc. Compositions and methods for modulating atp2a2 expression
US10837014B2 (en) 2012-05-16 2020-11-17 Translate Bio Ma, Inc. Compositions and methods for modulating SMN gene family expression
EP2850185A4 (en) 2012-05-16 2015-12-30 Rana Therapeutics Inc COMPOSITIONS AND METHOD FOR MODULATING UTRN GENE EXPRESSION
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