JP2022542828A5 - - Google Patents

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Publication number
JP2022542828A5
JP2022542828A5 JP2022502941A JP2022502941A JP2022542828A5 JP 2022542828 A5 JP2022542828 A5 JP 2022542828A5 JP 2022502941 A JP2022502941 A JP 2022502941A JP 2022502941 A JP2022502941 A JP 2022502941A JP 2022542828 A5 JP2022542828 A5 JP 2022542828A5
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JP
Japan
Prior art keywords
aav
promoter sequence
aav serotype
natural
vector
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022502941A
Other languages
English (en)
Japanese (ja)
Other versions
JP2022542828A (ja
Filing date
Publication date
Priority claimed from US16/512,194 external-priority patent/US10557149B1/en
Application filed filed Critical
Publication of JP2022542828A publication Critical patent/JP2022542828A/ja
Publication of JP2022542828A5 publication Critical patent/JP2022542828A5/ja
Priority to JP2024231646A priority Critical patent/JP2025032006A/ja
Pending legal-status Critical Current

Links

JP2022502941A 2019-07-15 2020-01-24 組換え修飾アデノ随伴ウイルスのパッケージング効率を改善するための組換え修飾アデノ随伴ウイルスヘルパーベクターおよびそれらの使用 Pending JP2022542828A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024231646A JP2025032006A (ja) 2019-07-15 2024-12-27 組換え修飾アデノ随伴ウイルスのパッケージング効率を改善するための組換え修飾アデノ随伴ウイルスヘルパーベクターおよびそれらの使用

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US16/512,194 2019-07-15
US16/512,194 US10557149B1 (en) 2019-07-15 2019-07-15 Recombinantly-modified adeno-associated virus helper vectors and their use to improve the packaging efficiency of recombinantly-modified adeno-associated virus
PCT/US2020/014945 WO2021011029A1 (en) 2019-07-15 2020-01-24 Recombinantly-modified adeno-associated virus helper vectors and their use to improve the packaging efficiency of recombinantly-modified adeno-associated virus

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024231646A Division JP2025032006A (ja) 2019-07-15 2024-12-27 組換え修飾アデノ随伴ウイルスのパッケージング効率を改善するための組換え修飾アデノ随伴ウイルスヘルパーベクターおよびそれらの使用

Publications (2)

Publication Number Publication Date
JP2022542828A JP2022542828A (ja) 2022-10-07
JP2022542828A5 true JP2022542828A5 (https=) 2023-02-01

Family

ID=69410866

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2022502941A Pending JP2022542828A (ja) 2019-07-15 2020-01-24 組換え修飾アデノ随伴ウイルスのパッケージング効率を改善するための組換え修飾アデノ随伴ウイルスヘルパーベクターおよびそれらの使用
JP2024231646A Pending JP2025032006A (ja) 2019-07-15 2024-12-27 組換え修飾アデノ随伴ウイルスのパッケージング効率を改善するための組換え修飾アデノ随伴ウイルスヘルパーベクターおよびそれらの使用

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2024231646A Pending JP2025032006A (ja) 2019-07-15 2024-12-27 組換え修飾アデノ随伴ウイルスのパッケージング効率を改善するための組換え修飾アデノ随伴ウイルスヘルパーベクターおよびそれらの使用

Country Status (7)

Country Link
US (3) US10557149B1 (https=)
EP (1) EP3999625A4 (https=)
JP (2) JP2022542828A (https=)
KR (1) KR20220034212A (https=)
CN (2) CN114450393B (https=)
AU (1) AU2020315770A1 (https=)
WO (1) WO2021011029A1 (https=)

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CN114657153A (zh) * 2022-05-24 2022-06-24 上海健士拜生物科技有限公司 rAAV重组包装质粒、用于rAAV包装的质粒系统和rAAV的制备方法
WO2024160232A1 (zh) * 2023-02-01 2024-08-08 纽福斯(苏州)生物科技有限公司 质粒包装系统及其应用
CN118633572A (zh) * 2023-03-06 2024-09-13 北京锦篮基因科技有限公司 神经元核内包涵体病小鼠模型构建方法及应用
CN117925663A (zh) * 2023-12-04 2024-04-26 广州派真生物技术有限公司 一种用于重组腺相关病毒包装的质粒系统及其应用
CN117660534B (zh) * 2023-12-13 2024-05-07 广州派真生物技术有限公司 一种降低重组腺相关病毒中宿主细胞dna残留的辅助质粒及应用
CN120118956A (zh) * 2025-03-05 2025-06-10 广州派真生物技术有限公司 一种高产aav的包装辅助质粒及应用

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