KR20220034212A - 재조합으로 변형된 아데노 연관 바이러스 헬퍼 벡터 및 재조합으로 변형된 아데노 연관 바이러스의 패키징 효율을 개선하기 위한 그의 용도 - Google Patents

재조합으로 변형된 아데노 연관 바이러스 헬퍼 벡터 및 재조합으로 변형된 아데노 연관 바이러스의 패키징 효율을 개선하기 위한 그의 용도 Download PDF

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KR20220034212A
KR20220034212A KR1020227004887A KR20227004887A KR20220034212A KR 20220034212 A KR20220034212 A KR 20220034212A KR 1020227004887 A KR1020227004887 A KR 1020227004887A KR 20227004887 A KR20227004887 A KR 20227004887A KR 20220034212 A KR20220034212 A KR 20220034212A
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aav
serotype
promoter sequence
native
raav
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Korean (ko)
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퀴즈하오 왕
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찰스리버레보레토리스,인코포레이티드
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KR1020227004887A 2019-07-15 2020-01-24 재조합으로 변형된 아데노 연관 바이러스 헬퍼 벡터 및 재조합으로 변형된 아데노 연관 바이러스의 패키징 효율을 개선하기 위한 그의 용도 Pending KR20220034212A (ko)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US16/512,194 2019-07-15
US16/512,194 US10557149B1 (en) 2019-07-15 2019-07-15 Recombinantly-modified adeno-associated virus helper vectors and their use to improve the packaging efficiency of recombinantly-modified adeno-associated virus
PCT/US2020/014945 WO2021011029A1 (en) 2019-07-15 2020-01-24 Recombinantly-modified adeno-associated virus helper vectors and their use to improve the packaging efficiency of recombinantly-modified adeno-associated virus

Publications (1)

Publication Number Publication Date
KR20220034212A true KR20220034212A (ko) 2022-03-17

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KR1020227004887A Pending KR20220034212A (ko) 2019-07-15 2020-01-24 재조합으로 변형된 아데노 연관 바이러스 헬퍼 벡터 및 재조합으로 변형된 아데노 연관 바이러스의 패키징 효율을 개선하기 위한 그의 용도

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US (3) US10557149B1 (https=)
EP (1) EP3999625A4 (https=)
JP (2) JP2022542828A (https=)
KR (1) KR20220034212A (https=)
CN (2) CN114450393B (https=)
AU (1) AU2020315770A1 (https=)
WO (1) WO2021011029A1 (https=)

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WO2024160232A1 (zh) * 2023-02-01 2024-08-08 纽福斯(苏州)生物科技有限公司 质粒包装系统及其应用
CN118633572A (zh) * 2023-03-06 2024-09-13 北京锦篮基因科技有限公司 神经元核内包涵体病小鼠模型构建方法及应用
CN117925663A (zh) * 2023-12-04 2024-04-26 广州派真生物技术有限公司 一种用于重组腺相关病毒包装的质粒系统及其应用
CN117660534B (zh) * 2023-12-13 2024-05-07 广州派真生物技术有限公司 一种降低重组腺相关病毒中宿主细胞dna残留的辅助质粒及应用
CN120118956A (zh) * 2025-03-05 2025-06-10 广州派真生物技术有限公司 一种高产aav的包装辅助质粒及应用

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JP2022542828A (ja) 2022-10-07
EP3999625A1 (en) 2022-05-25
US20220290178A1 (en) 2022-09-15
CN114450393A (zh) 2022-05-06
US20210017538A1 (en) 2021-01-21
US10557149B1 (en) 2020-02-11
JP2025032006A (ja) 2025-03-07
CN121472168A (zh) 2026-02-06
US11001859B2 (en) 2021-05-11
WO2021011029A1 (en) 2021-01-21
EP3999625A4 (en) 2023-08-30
CN114450393B (zh) 2025-09-12

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