JP2022542828A - 組換え修飾アデノ随伴ウイルスのパッケージング効率を改善するための組換え修飾アデノ随伴ウイルスヘルパーベクターおよびそれらの使用 - Google Patents

組換え修飾アデノ随伴ウイルスのパッケージング効率を改善するための組換え修飾アデノ随伴ウイルスヘルパーベクターおよびそれらの使用 Download PDF

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JP2022542828A
JP2022542828A JP2022502941A JP2022502941A JP2022542828A JP 2022542828 A JP2022542828 A JP 2022542828A JP 2022502941 A JP2022502941 A JP 2022502941A JP 2022502941 A JP2022502941 A JP 2022502941A JP 2022542828 A JP2022542828 A JP 2022542828A
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raav
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ワング，チィツァオ
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チャールズ・リバー・ラボラトリーズ・インコーポレーテッド
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JP2022502941A 2019-07-15 2020-01-24 組換え修飾アデノ随伴ウイルスのパッケージング効率を改善するための組換え修飾アデノ随伴ウイルスヘルパーベクターおよびそれらの使用 Pending JP2022542828A (ja)

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JP2024231646A JP2025032006A (ja) 2019-07-15 2024-12-27 組換え修飾アデノ随伴ウイルスのパッケージング効率を改善するための組換え修飾アデノ随伴ウイルスヘルパーベクターおよびそれらの使用

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US16/512,194 2019-07-15
US16/512,194 US10557149B1 (en) 2019-07-15 2019-07-15 Recombinantly-modified adeno-associated virus helper vectors and their use to improve the packaging efficiency of recombinantly-modified adeno-associated virus
PCT/US2020/014945 WO2021011029A1 (en) 2019-07-15 2020-01-24 Recombinantly-modified adeno-associated virus helper vectors and their use to improve the packaging efficiency of recombinantly-modified adeno-associated virus

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US (3) US10557149B1 (https=)
EP (1) EP3999625A4 (https=)
JP (2) JP2022542828A (https=)
KR (1) KR20220034212A (https=)
CN (2) CN114450393B (https=)
AU (1) AU2020315770A1 (https=)
WO (1) WO2021011029A1 (https=)

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CN114657153A (zh) * 2022-05-24 2022-06-24 上海健士拜生物科技有限公司 rAAV重组包装质粒、用于rAAV包装的质粒系统和rAAV的制备方法
WO2024160232A1 (zh) * 2023-02-01 2024-08-08 纽福斯(苏州)生物科技有限公司 质粒包装系统及其应用
CN118633572A (zh) * 2023-03-06 2024-09-13 北京锦篮基因科技有限公司 神经元核内包涵体病小鼠模型构建方法及应用
CN117925663A (zh) * 2023-12-04 2024-04-26 广州派真生物技术有限公司 一种用于重组腺相关病毒包装的质粒系统及其应用
CN117660534B (zh) * 2023-12-13 2024-05-07 广州派真生物技术有限公司 一种降低重组腺相关病毒中宿主细胞dna残留的辅助质粒及应用
CN120118956A (zh) * 2025-03-05 2025-06-10 广州派真生物技术有限公司 一种高产aav的包装辅助质粒及应用

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US11001859B2 (en) 2021-05-11
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