JP2022553307A5 - - Google Patents

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Publication number
JP2022553307A5
JP2022553307A5 JP2022523408A JP2022523408A JP2022553307A5 JP 2022553307 A5 JP2022553307 A5 JP 2022553307A5 JP 2022523408 A JP2022523408 A JP 2022523408A JP 2022523408 A JP2022523408 A JP 2022523408A JP 2022553307 A5 JP2022553307 A5 JP 2022553307A5
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JP
Japan
Application number
JP2022523408A
Other languages
Japanese (ja)
Other versions
JP2022553307A (ja
JPWO2021081201A5 (https=
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/056860 external-priority patent/WO2021081201A1/en
Publication of JP2022553307A publication Critical patent/JP2022553307A/ja
Publication of JPWO2021081201A5 publication Critical patent/JPWO2021081201A5/ja
Publication of JP2022553307A5 publication Critical patent/JP2022553307A5/ja
Pending legal-status Critical Current

Links

JP2022523408A 2019-10-22 2020-10-22 プログラニュリン関連神経変性疾患または障害の治療のためのアデノ随伴ウイルス(aav)システム Pending JP2022553307A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962924340P 2019-10-22 2019-10-22
US62/924,340 2019-10-22
PCT/US2020/056860 WO2021081201A1 (en) 2019-10-22 2020-10-22 Adeno-associated virus (aav) systems for treatment of progranulin associated neurodegeneative diseases or disorders

Publications (3)

Publication Number Publication Date
JP2022553307A JP2022553307A (ja) 2022-12-22
JPWO2021081201A5 JPWO2021081201A5 (https=) 2023-10-30
JP2022553307A5 true JP2022553307A5 (https=) 2023-10-30

Family

ID=75620215

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022523408A Pending JP2022553307A (ja) 2019-10-22 2020-10-22 プログラニュリン関連神経変性疾患または障害の治療のためのアデノ随伴ウイルス(aav)システム

Country Status (10)

Country Link
US (2) US20210147872A1 (https=)
EP (1) EP4048799A4 (https=)
JP (1) JP2022553307A (https=)
KR (1) KR20230019402A (https=)
CN (1) CN115715327A (https=)
AU (1) AU2020371662A1 (https=)
CA (1) CA3158516A1 (https=)
IL (1) IL292382A (https=)
MX (1) MX2022004812A (https=)
WO (1) WO2021081201A1 (https=)

Families Citing this family (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2021533126A (ja) * 2018-07-31 2021-12-02 コーネル・ユニバーシティーCornell University 臓器機能を制御するための遺伝子治療方法
KR20230128001A (ko) * 2020-12-01 2023-09-01 더 트러스티스 오브 더 유니버시티 오브 펜실베니아 엔젤만 증후군의 치료를 위한 조성물 및 이의 용도
US20240033332A1 (en) * 2020-12-17 2024-02-01 Kyoto University Agent for activating a neuron
WO2024035649A1 (en) * 2022-08-08 2024-02-15 Shape Therapeutics Inc. Compositions for progranulin expression and methods of use thereof
KR20250131772A (ko) * 2022-11-13 2025-09-03 알렉시온 파마 인터내셔널 오퍼레이션즈 리미티드 전두측두엽 치매에 대한 유전자 요법
WO2025251041A1 (en) * 2024-05-31 2025-12-04 Bluerock Therapeutics Lp METHODS AND COMPOSITIONS FOR TREATING PROGRANULIN DEFICIENCIES USING iPSC-DERIVED CELLS

Family Cites Families (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2009089635A1 (en) * 2008-01-16 2009-07-23 Neurodyn, Inc. Treating neurodegenerative diseases with progranulin (pgrn)
JP5879256B2 (ja) * 2009-05-02 2016-03-08 ジェンザイム・コーポレーション 神経変性障害のための遺伝子治療
AU2013243948A1 (en) * 2012-04-02 2014-10-30 Moderna Therapeutics, Inc. Modified polynucleotides for the production of proteins associated with human disease
WO2016125330A1 (ja) * 2015-02-02 2016-08-11 原 英彰 網膜再生促進薬
WO2017151884A1 (en) * 2016-03-02 2017-09-08 The Children's Hospital Of Philadelphia Therapy for frontotemporal dementia
WO2018136680A1 (en) * 2017-01-19 2018-07-26 New York University Progranulin and progranulin derivatives in treating impaired fracture healing
EP3692075A4 (en) * 2017-10-03 2022-02-09 Prevail Therapeutics, Inc. GENE THERAPIES FOR LYSOSOMAL DISEASES
KR102709597B1 (ko) * 2017-10-03 2024-09-26 프리베일 테라퓨틱스, 인크. 리소좀 장애를 위한 유전자 요법
US20220111005A1 (en) * 2019-02-01 2022-04-14 Avrobio, Inc. Compositions and methods for treating neurocognitive disorders
BR112021015817A2 (pt) * 2019-02-22 2021-10-13 The Trustees Of The University Of Pennsylvania Vírus adeno-associado recombinante para tratamento de neurodegeneração com início na idade adulta associado a grn

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