JP2022518931A5 - - Google Patents
Info
- Publication number
- JP2022518931A5 JP2022518931A5 JP2021544194A JP2021544194A JP2022518931A5 JP 2022518931 A5 JP2022518931 A5 JP 2022518931A5 JP 2021544194 A JP2021544194 A JP 2021544194A JP 2021544194 A JP2021544194 A JP 2021544194A JP 2022518931 A5 JP2022518931 A5 JP 2022518931A5
- Authority
- JP
- Japan
- Prior art keywords
- composition according
- aav
- vector
- approximately
- sequence
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2025030051A JP2025098018A (ja) | 2019-02-01 | 2025-02-27 | 遅発型小児性神経セロイドリポフスチン沈着症２型に対するａａｖベクター治療法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962800131P | 2019-02-01 | 2019-02-01 | |
| US62/800,131 | 2019-02-01 | ||
| PCT/US2020/016235 WO2020160486A1 (en) | 2019-02-01 | 2020-01-31 | Aav vector treatment methods for late infantile neuronal ceroid lipofuscinosis type 2 |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025030051A Division JP2025098018A (ja) | 2019-02-01 | 2025-02-27 | 遅発型小児性神経セロイドリポフスチン沈着症２型に対するａａｖベクター治療法 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022518931A JP2022518931A (ja) | 2022-03-17 |
| JP2022518931A5 true JP2022518931A5 (https=) | 2023-05-23 |
Family
ID=71841678
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021544194A Pending JP2022518931A (ja) | 2019-02-01 | 2020-01-31 | 遅発型小児性神経セロイドリポフスチン沈着症２型に対するａａｖベクター治療法 |
| JP2025030051A Withdrawn JP2025098018A (ja) | 2019-02-01 | 2025-02-27 | 遅発型小児性神経セロイドリポフスチン沈着症２型に対するａａｖベクター治療法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025030051A Withdrawn JP2025098018A (ja) | 2019-02-01 | 2025-02-27 | 遅発型小児性神経セロイドリポフスチン沈着症２型に対するａａｖベクター治療法 |
Country Status (9)
| Country | Link |
|---|---|
| US (1) | US20220184188A1 (https=) |
| EP (1) | EP3917522A4 (https=) |
| JP (2) | JP2022518931A (https=) |
| CN (1) | CN113891712A (https=) |
| AU (1) | AU2020215592A1 (https=) |
| BR (1) | BR112021015050A2 (https=) |
| CA (1) | CA3127889A1 (https=) |
| MX (1) | MX2021009250A (https=) |
| WO (1) | WO2020160486A1 (https=) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA3132379A1 (en) * | 2019-03-22 | 2020-10-01 | Rush University Medical Center | Combination of nasal gene delivery and oral cinnamic acid, oleamide or gemfibrozil for lysosomal storage disorders |
| AU2022337146A1 (en) | 2021-09-03 | 2024-03-14 | Tacit Therapeutics, Inc. | Rna editing via recruitment of spliceosome components |
| WO2025231406A1 (en) * | 2024-05-02 | 2025-11-06 | The Children's Hospital Of Philadelphia | Methods to increase transduction of ependyma cells in brain |
Family Cites Families (7)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP2132309A4 (en) * | 2007-02-23 | 2011-01-05 | Univ Florida | COMPOSITIONS AND METHODS OF TREATING GLYCOLOGICAL MEMORY DISEASES |
| WO2012135857A1 (en) * | 2011-03-31 | 2012-10-04 | University Of Iowa Research Foundation | Methods and compositions for treating brain diseases |
| US20140271550A1 (en) * | 2013-03-14 | 2014-09-18 | The Trustees Of The University Of Pennsylvania | Constructs and Methods for Delivering Molecules via Viral Vectors with Blunted Innate Immune Responses |
| EP3024497B1 (en) * | 2013-07-26 | 2021-01-13 | University of Iowa Research Foundation | Methods and compositions for treating brain diseases |
| US10900053B2 (en) * | 2014-11-21 | 2021-01-26 | University Of Florida Research Foundation, Incorporated | Genome-modified recombinant adeno-associated virus vectors |
| KR102738860B1 (ko) * | 2015-10-23 | 2024-12-04 | 유니버시티 오브 아이오와 리써치 파운데이션 | 리소좀 축적 질환 (lsd)을 갖는 포유동물의 치료 방법에 사용하기 위한 aav 입자를 포함하는 약제학적 조성물 |
| CA3041548A1 (en) * | 2016-11-04 | 2018-05-11 | The Children's Hospital Of Philadelphia | Gene transfer compositions, methods and uses for treating neurodegenerative diseases |
-
2020
- 2020-01-31 WO PCT/US2020/016235 patent/WO2020160486A1/en not_active Ceased
- 2020-01-31 US US17/310,378 patent/US20220184188A1/en not_active Abandoned
- 2020-01-31 JP JP2021544194A patent/JP2022518931A/ja active Pending
- 2020-01-31 AU AU2020215592A patent/AU2020215592A1/en not_active Abandoned
- 2020-01-31 BR BR112021015050-1A patent/BR112021015050A2/pt unknown
- 2020-01-31 CN CN202080024872.5A patent/CN113891712A/zh active Pending
- 2020-01-31 CA CA3127889A patent/CA3127889A1/en active Pending
- 2020-01-31 EP EP20749051.7A patent/EP3917522A4/en not_active Withdrawn
- 2020-01-31 MX MX2021009250A patent/MX2021009250A/es unknown
-
2025
- 2025-02-27 JP JP2025030051A patent/JP2025098018A/ja not_active Withdrawn
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