JP2024504611A5 - - Google Patents
Info
- Publication number
- JP2024504611A5 JP2024504611A5 JP2023542653A JP2023542653A JP2024504611A5 JP 2024504611 A5 JP2024504611 A5 JP 2024504611A5 JP 2023542653 A JP2023542653 A JP 2023542653A JP 2023542653 A JP2023542653 A JP 2023542653A JP 2024504611 A5 JP2024504611 A5 JP 2024504611A5
- Authority
- JP
- Japan
- Prior art keywords
- sequence
- seq
- gla
- nucleic acid
- signal peptide
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Withdrawn
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163137235P | 2021-01-14 | 2021-01-14 | |
| US63/137,235 | 2021-01-14 | ||
| US202163264356P | 2021-11-19 | 2021-11-19 | |
| US63/264,356 | 2021-11-19 | ||
| PCT/US2022/070184 WO2022155665A1 (en) | 2021-01-14 | 2022-01-13 | Compositions and methods for treating fabry disease |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024504611A JP2024504611A (ja) | 2024-02-01 |
| JP2024504611A5 true JP2024504611A5 (https=) | 2025-01-08 |
Family
ID=82448637
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023542653A Withdrawn JP2024504611A (ja) | 2021-01-14 | 2022-01-13 | ファブリー病を治療するための組成物および方法 |
Country Status (12)
| Country | Link |
|---|---|
| US (1) | US20240301380A1 (https=) |
| EP (1) | EP4277988A4 (https=) |
| JP (1) | JP2024504611A (https=) |
| KR (1) | KR20230131246A (https=) |
| AU (1) | AU2022207185A1 (https=) |
| CA (1) | CA3208153A1 (https=) |
| CL (1) | CL2023002015A1 (https=) |
| CO (1) | CO2023010599A2 (https=) |
| IL (1) | IL304273A (https=) |
| MX (1) | MX2023008362A (https=) |
| PE (1) | PE20240915A1 (https=) |
| WO (1) | WO2022155665A1 (https=) |
Families Citing this family (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP4426846A4 (en) * | 2021-11-03 | 2025-11-05 | Sangamo Therapeutics Inc | METHODS OF USING VIRAL VECTOR CONSTRUCTIONS FOR THE TREATMENT OF FABRY DISEASE |
| KR20250161626A (ko) * | 2023-03-20 | 2025-11-17 | 스파크 테라퓨틱스, 인코포레이티드 | Ppt1 유전자 치료 |
| US20240360431A1 (en) * | 2023-04-30 | 2024-10-31 | Sichuan Real&Best Biotech Co., Ltd. | Engineered alpha-galactosidase a (a-gal a) peptides and functional variants thereof and associated methods of treating fabry disease |
| CN117551636B (zh) * | 2023-04-30 | 2024-11-08 | 四川至善唯新生物科技有限公司 | 工程化α-GAL A肽及其功能变体和治疗法布里病的相关方法 |
| WO2025264565A1 (en) * | 2024-06-17 | 2025-12-26 | Spark Therapeutics, Inc. | Promoters |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2013151665A2 (en) * | 2012-04-02 | 2013-10-10 | modeRNA Therapeutics | Modified polynucleotides for the production of proteins associated with human disease |
| WO2017201328A1 (en) * | 2016-05-18 | 2017-11-23 | Modernatx, Inc. | POLYNUCLEOTIDES ENCODING α-GALACTOSIDASE A FOR THE TREATMENT OF FABRY DISEASE |
| KR102712926B1 (ko) * | 2016-10-20 | 2024-10-07 | 상가모 테라퓨틱스, 인코포레이티드 | 파브리병의 치료를 위한 방법 및 조성물 |
| MY207355A (en) * | 2018-05-16 | 2025-02-21 | Spark Therapeutics Inc | Codon-optimized acid lpha-glucosidase expression cassettes and methods of using same |
| KR20220022107A (ko) * | 2018-12-05 | 2022-02-24 | 아베오나 테라퓨틱스 인코퍼레이티드 | 유전자 전달을 위한 재조합 아데노-연관 바이러스 벡터 |
| US12163425B2 (en) * | 2020-03-13 | 2024-12-10 | Baker Hughes Oilfield Operations Llc | Automated geosteering based on a distance to oil-water contact |
-
2022
- 2022-01-13 MX MX2023008362A patent/MX2023008362A/es unknown
- 2022-01-13 KR KR1020237027400A patent/KR20230131246A/ko not_active Withdrawn
- 2022-01-13 CA CA3208153A patent/CA3208153A1/en active Pending
- 2022-01-13 PE PE2023002056A patent/PE20240915A1/es unknown
- 2022-01-13 JP JP2023542653A patent/JP2024504611A/ja not_active Withdrawn
- 2022-01-13 WO PCT/US2022/070184 patent/WO2022155665A1/en not_active Ceased
- 2022-01-13 US US18/261,285 patent/US20240301380A1/en active Pending
- 2022-01-13 AU AU2022207185A patent/AU2022207185A1/en not_active Abandoned
- 2022-01-13 EP EP22740258.3A patent/EP4277988A4/en not_active Withdrawn
-
2023
- 2023-07-05 IL IL304273A patent/IL304273A/en unknown
- 2023-07-11 CL CL2023002015A patent/CL2023002015A1/es unknown
- 2023-08-14 CO CONC2023/0010599A patent/CO2023010599A2/es unknown
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| JP2024504611A5 (https=) | ||
| JP2024009857A5 (https=) | ||
| JP2021106619A5 (https=) | ||
| JP2021087431A5 (https=) | ||
| JP2022508182A5 (https=) | ||
| JP2021523718A5 (https=) | ||
| JP2022549380A5 (https=) | ||
| JP7162021B2 (ja) | 筋ジストロフィーを治療するためのマイクロジストロフィン断片のアデノ随伴ウイルスベクター送達 | |
| JP2022060228A5 (https=) | ||
| IL273261B2 (en) | Adeno-associated virus variant capsids and methods of using them | |
| JP2019116492A5 (https=) | ||
| JP2007507223A5 (https=) | ||
| JP2024506266A5 (https=) | ||
| IL299325B1 (en) | Variants of acid alpha-glucosidase and their uses | |
| JP2022551744A5 (https=) | ||
| RU2018116076A (ru) | Модифицированные гены атаксии фридрейха и векторы для генной терапии | |
| JP2022541070A5 (https=) | ||
| JP2023537358A5 (https=) | ||
| JP2023524024A5 (https=) | ||
| JP2024508696A5 (https=) | ||
| JP2023520763A5 (https=) | ||
| JP2023549124A5 (https=) | ||
| JP2021534766A5 (https=) | ||
| JP2025513785A5 (https=) | ||
| WO2024119102A1 (en) | Adeno-associated viral vectors for proper packaging of repetitive elements |