JP2021534766A5 - - Google Patents
Info
- Publication number
- JP2021534766A5 JP2021534766A5 JP2021510129A JP2021510129A JP2021534766A5 JP 2021534766 A5 JP2021534766 A5 JP 2021534766A5 JP 2021510129 A JP2021510129 A JP 2021510129A JP 2021510129 A JP2021510129 A JP 2021510129A JP 2021534766 A5 JP2021534766 A5 JP 2021534766A5
- Authority
- JP
- Japan
- Prior art keywords
- recombinant aav
- capsid protein
- promoter
- item
- virus particles
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2024174226A JP2025004107A (ja) | 2018-08-30 | 2024-10-03 | ガラクトース血症の処置のための遺伝子治療 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862725225P | 2018-08-30 | 2018-08-30 | |
| US62/725,225 | 2018-08-30 | ||
| PCT/US2019/049157 WO2020047472A1 (en) | 2018-08-30 | 2019-08-30 | Gene therapy for the treatment of galactosemia |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024174226A Division JP2025004107A (ja) | 2018-08-30 | 2024-10-03 | ガラクトース血症の処置のための遺伝子治療 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2021534766A JP2021534766A (ja) | 2021-12-16 |
| JP2021534766A5 true JP2021534766A5 (https=) | 2022-09-06 |
| JP7688572B2 JP7688572B2 (ja) | 2025-06-04 |
Family
ID=69643062
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021510129A Active JP7688572B2 (ja) | 2018-08-30 | 2019-08-30 | ガラクトース血症の処置のための遺伝子治療 |
| JP2024174226A Withdrawn JP2025004107A (ja) | 2018-08-30 | 2024-10-03 | ガラクトース血症の処置のための遺伝子治療 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024174226A Withdrawn JP2025004107A (ja) | 2018-08-30 | 2024-10-03 | ガラクトース血症の処置のための遺伝子治療 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US20210299275A1 (https=) |
| EP (1) | EP3844294A4 (https=) |
| JP (2) | JP7688572B2 (https=) |
| KR (1) | KR20210052469A (https=) |
| CN (2) | CN112867798A (https=) |
| AU (2) | AU2019328573A1 (https=) |
| BR (1) | BR112021003174A2 (https=) |
| CA (1) | CA3110290A1 (https=) |
| MX (1) | MX2021002041A (https=) |
| SG (1) | SG11202101819QA (https=) |
| WO (1) | WO2020047472A1 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP3765624A4 (en) * | 2018-03-16 | 2022-05-25 | Research Institute at Nationwide Children's Hospital | Increasing tissue specific gene delivery by capsid modification |
| WO2023279108A1 (en) * | 2021-07-01 | 2023-01-05 | Bridgebio Gene Therapy Research, Inc. | Gene therapy for galactosemia |
| WO2023034940A2 (en) * | 2021-09-01 | 2023-03-09 | Jaguar Gene Therapy, Llc | Adeno-associated vectors and virions to treat galactosemia and methods of use and manufacture |
| US20240358856A1 (en) * | 2021-09-01 | 2024-10-31 | Jaguar Gene Therapy, Llc | Adeno-associated vectors and virions to treat galactosemia and methods of use and manufacture |
Family Cites Families (13)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2001096587A2 (en) * | 2000-06-13 | 2001-12-20 | The Children's Hospital Of Philadelphia | Methods for administering recombinant adeno-associated virus virions to humans previously exposed to adeno-associated virus |
| US7795002B2 (en) * | 2000-06-28 | 2010-09-14 | Glycofi, Inc. | Production of galactosylated glycoproteins in lower eukaryotes |
| AU2002308540A1 (en) * | 2001-05-01 | 2002-11-11 | Genstar Therapeutics Corp. | Mini-adenoviral vector and methods of using same |
| WO2003088899A2 (en) * | 2002-04-05 | 2003-10-30 | The Children's Hospital Of Philadelphia | Methods for the production of chimeric adeno-associated virus (aav) vectors, compositions of chimeric aav vectors, and methods of use thereof |
| SI1633772T1 (sl) * | 2003-06-19 | 2016-06-30 | Genzyme Corporation | AAV virioni z zmanjšano imunoreaktivnostjo in uporaba za ta namen |
| WO2005117576A2 (en) * | 2004-05-28 | 2005-12-15 | University Of Pittsburgh Of The Commonwealth System Of Higher Education | Modification of sugar metabolic process in transgenic cells, tissues and animals |
| CA2733104C (en) * | 2008-08-07 | 2015-07-14 | Her Majesty The Queen In Right Of Canada As Represented By The Minister Of Health | Optimized promoter sequence |
| US20110223635A1 (en) * | 2008-08-11 | 2011-09-15 | Karl Deisseroth | Method and Composition for Controlling Gene Expression |
| JP6188728B2 (ja) * | 2012-02-07 | 2017-08-30 | グローバル・バイオ・セラピューティクス・インコーポレイテッドＧｌｏｂａｌ Ｂｉｏ Ｔｈｅｒａｐｅｕｔｉｃｓ，Ｉｎｃ． | 核酸送達の区画化方法ならびにその組成物および使用 |
| EP3388834B1 (en) * | 2013-03-15 | 2020-04-15 | Translate Bio, Inc. | Synergistic enhancement of the delivery of nucleic acids via blended formulations |
| WO2017191274A2 (en) * | 2016-05-04 | 2017-11-09 | Curevac Ag | Rna encoding a therapeutic protein |
| US11001861B2 (en) * | 2016-05-18 | 2021-05-11 | Modernatx, Inc. | Polynucleotides encoding galactose-1-phosphate uridylyltransferase for the treatment of galactosemia type 1 |
| MX2018014256A (es) * | 2016-05-20 | 2019-08-16 | Harvard College | Metodos de terapia genica para enfermedades y condiciones relacionadas con la edad. |
-
2019
- 2019-08-30 BR BR112021003174-0A patent/BR112021003174A2/pt unknown
- 2019-08-30 AU AU2019328573A patent/AU2019328573A1/en not_active Abandoned
- 2019-08-30 MX MX2021002041A patent/MX2021002041A/es unknown
- 2019-08-30 EP EP19854595.6A patent/EP3844294A4/en active Pending
- 2019-08-30 SG SG11202101819QA patent/SG11202101819QA/en unknown
- 2019-08-30 CN CN201980069706.4A patent/CN112867798A/zh active Pending
- 2019-08-30 KR KR1020217007850A patent/KR20210052469A/ko active Pending
- 2019-08-30 WO PCT/US2019/049157 patent/WO2020047472A1/en not_active Ceased
- 2019-08-30 CA CA3110290A patent/CA3110290A1/en active Pending
- 2019-08-30 JP JP2021510129A patent/JP7688572B2/ja active Active
- 2019-08-30 US US17/272,194 patent/US20210299275A1/en active Pending
- 2019-08-30 CN CN202510783197.9A patent/CN120843445A/zh active Pending
-
2024
- 2024-10-03 JP JP2024174226A patent/JP2025004107A/ja not_active Withdrawn
-
2025
- 2025-12-17 AU AU2025283486A patent/AU2025283486A1/en active Pending
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