JP2023537358A5 - - Google Patents
Info
- Publication number
- JP2023537358A5 JP2023537358A5 JP2023507927A JP2023507927A JP2023537358A5 JP 2023537358 A5 JP2023537358 A5 JP 2023537358A5 JP 2023507927 A JP2023507927 A JP 2023507927A JP 2023507927 A JP2023507927 A JP 2023507927A JP 2023537358 A5 JP2023537358 A5 JP 2023537358A5
- Authority
- JP
- Japan
- Prior art keywords
- nucleic acid
- seq
- acid sequence
- hsa
- mir
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| CNPCT/CN2020/107173 | 2020-08-05 | ||
| CN2020107173 | 2020-08-05 | ||
| CN2020138056 | 2020-12-21 | ||
| CNPCT/CN2020/138056 | 2020-12-21 | ||
| PCT/CN2021/110521 WO2022028472A1 (en) | 2020-08-05 | 2021-08-04 | Nucleic acid constructs and uses thereof for treating spinal muscular atrophy |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023537358A JP2023537358A (ja) | 2023-08-31 |
| JP2023537358A5 true JP2023537358A5 (https=) | 2024-08-13 |
Family
ID=80120030
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023507927A Pending JP2023537358A (ja) | 2020-08-05 | 2021-08-04 | 核酸構築物及び脊髄性筋委縮症治療のためのその使用 |
Country Status (9)
| Country | Link |
|---|---|
| US (1) | US20230293730A1 (https=) |
| EP (1) | EP4192518A4 (https=) |
| JP (1) | JP2023537358A (https=) |
| KR (1) | KR20230044522A (https=) |
| CN (1) | CN116685329B (https=) |
| AU (1) | AU2021323289A1 (https=) |
| CA (1) | CA3190601A1 (https=) |
| IL (1) | IL300277A (https=) |
| WO (1) | WO2022028472A1 (https=) |
Families Citing this family (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US12612627B2 (en) * | 2020-04-20 | 2026-04-28 | Regents Of The University Of Minnesota | Compositions and methods for increasing sodium current in cardiac cells |
| WO2023219394A1 (ko) * | 2022-05-10 | 2023-11-16 | 서울대학교산학협력단 | 인간 smn1 단백질 변이체 및 이의 용도 |
| EP4577662A1 (en) * | 2022-08-24 | 2025-07-02 | Beacon Therapeutics (USA), Inc. | Methods and compositions for the production of recombinant adeno-associated virus (raav) vectors |
| EP4711461A1 (en) * | 2023-05-12 | 2026-03-18 | Genecombio Ltd. | Viral vector carrying smn gene expression cassette and use thereof |
| CN118685413B (zh) * | 2024-08-28 | 2025-02-07 | 杭州嘉因生物科技有限公司 | 下调内源性smn的诱导型稳定细胞株的构建及其应用 |
Family Cites Families (11)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN103820562B (zh) * | 2005-08-01 | 2015-05-13 | 俄亥俄州立大学研究基金会 | 用于乳腺癌的诊断、预后和治疗的基于MicroRNA的方法和组合物 |
| CN101787373B (zh) * | 2009-01-23 | 2013-06-19 | 中国人民解放军第二军医大学东方肝胆外科医院 | 一种携带外源基因在包装细胞中高效生产的重组病毒载体、其构建方法及其用途 |
| EP2561073B1 (en) * | 2010-04-23 | 2016-08-24 | University of Massachusetts | Cns targeting aav vectors and methods of use thereof |
| FR3004463A1 (fr) * | 2013-04-11 | 2014-10-17 | Genethon | Systeme d'expression pour une therapie genique selective |
| MX380973B (es) * | 2013-05-01 | 2025-03-12 | Genzyme Corp | Composiciones y metodos para tratar la atrofia muscular espinal. |
| WO2018146588A1 (en) * | 2017-02-08 | 2018-08-16 | Friedrich Miescher Institute For Biomedical Research | Synp88, a promoter for the specific expression of genes in retinal ganglion cells |
| JOP20190200A1 (ar) * | 2017-02-28 | 2019-08-27 | Univ Pennsylvania | تركيبات نافعة في معالجة ضمور العضل النخاعي |
| CN114908099B (zh) * | 2018-06-28 | 2024-07-02 | 北京锦篮基因科技有限公司 | 携带设计smn1基因表达框的重组腺相关病毒及应用 |
| CN111088284B (zh) * | 2019-05-31 | 2022-02-01 | 北京京谱迪基因科技有限公司 | 携带截短抗肌萎缩蛋白基因表达框的aav载体、制备方法及应用 |
| CN110616262A (zh) * | 2019-08-14 | 2019-12-27 | 深圳市人民医院 | 外泌体中microRNA在评估脑胶质瘤放疗效果中的用途 |
| CN113755524B (zh) * | 2020-06-02 | 2023-11-03 | 舒泰神（北京）生物制药股份有限公司 | 用于治疗脊髓性肌萎缩的腺相关病毒载体及其用途 |
-
2021
- 2021-08-04 WO PCT/CN2021/110521 patent/WO2022028472A1/en not_active Ceased
- 2021-08-04 CA CA3190601A patent/CA3190601A1/en active Pending
- 2021-08-04 IL IL300277A patent/IL300277A/en unknown
- 2021-08-04 KR KR1020237007688A patent/KR20230044522A/ko active Pending
- 2021-08-04 US US18/019,449 patent/US20230293730A1/en active Pending
- 2021-08-04 EP EP21852149.0A patent/EP4192518A4/en active Pending
- 2021-08-04 CN CN202180067807.5A patent/CN116685329B/zh active Active
- 2021-08-04 JP JP2023507927A patent/JP2023537358A/ja active Pending
- 2021-08-04 AU AU2021323289A patent/AU2021323289A1/en active Pending
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