JP2022531809A5 - - Google Patents

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Publication number
JP2022531809A5
JP2022531809A5 JP2021567820A JP2021567820A JP2022531809A5 JP 2022531809 A5 JP2022531809 A5 JP 2022531809A5 JP 2021567820 A JP2021567820 A JP 2021567820A JP 2021567820 A JP2021567820 A JP 2021567820A JP 2022531809 A5 JP2022531809 A5 JP 2022531809A5
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JP
Japan
Application number
JP2021567820A
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Japanese (ja)
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JPWO2020232297A5 (https=
JP2022531809A (ja
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Publication date
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Priority claimed from PCT/US2020/032978 external-priority patent/WO2020232297A1/en
Publication of JP2022531809A publication Critical patent/JP2022531809A/ja
Publication of JPWO2020232297A5 publication Critical patent/JPWO2020232297A5/ja
Publication of JP2022531809A5 publication Critical patent/JP2022531809A5/ja
Pending legal-status Critical Current

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JP2021567820A 2019-05-14 2020-05-14 ATPase媒介性疾患の処置のための組成物および方法 Pending JP2022531809A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962847416P 2019-05-14 2019-05-14
US62/847,416 2019-05-14
PCT/US2020/032978 WO2020232297A1 (en) 2019-05-14 2020-05-14 Compositions and methods for the treatment of atpase-mediated diseases

Publications (3)

Publication Number Publication Date
JP2022531809A JP2022531809A (ja) 2022-07-11
JPWO2020232297A5 JPWO2020232297A5 (https=) 2023-05-16
JP2022531809A5 true JP2022531809A5 (https=) 2023-05-16

Family

ID=73289760

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2021567820A Pending JP2022531809A (ja) 2019-05-14 2020-05-14 ATPase媒介性疾患の処置のための組成物および方法

Country Status (12)

Country Link
US (2) US11717560B2 (https=)
EP (1) EP3969597A4 (https=)
JP (1) JP2022531809A (https=)
KR (1) KR20220032005A (https=)
CN (1) CN114072514A (https=)
AU (1) AU2020274200A1 (https=)
BR (1) BR112021022951A2 (https=)
CA (1) CA3140049A1 (https=)
IL (1) IL287796A (https=)
MX (1) MX2021013913A (https=)
SG (1) SG11202112078TA (https=)
WO (1) WO2020232297A1 (https=)

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US20210363191A1 (en) 2018-04-03 2021-11-25 Stridebio, Inc. Antibody-evading virus vectors
BR112021018776A2 (pt) 2019-03-21 2021-11-30 Stridebio Inc Vetores de vírus adenoassociado recombinante
CN114072514A (zh) * 2019-05-14 2022-02-18 杜克大学 用于治疗atp酶介导的疾病的组合物和方法
KR20220083714A (ko) 2019-10-17 2022-06-20 스트라이드바이오 인코포레이티드 니만-피크 질환 c형의 치료를 위한 아데노-연관 바이러스 벡터
EP4200408A1 (en) 2020-08-19 2023-06-28 Sarepta Therapeutics, Inc. Adeno-associated virus vectors for treatment of rett syndrome
US20250144239A1 (en) * 2021-10-18 2025-05-08 Logicbio Therapeutics, Inc. Gene therapy for the treatment of wilson's disease
WO2023230466A1 (en) * 2022-05-23 2023-11-30 Lutsenka Svetlana Compositions and methods for treating wilson's disease
CN115851730A (zh) * 2022-11-16 2023-03-28 泰达国际心血管病医院 Myh6基因启动子变异及其应用与先天性心脏病基因检测试剂盒

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WO2001046226A2 (en) * 1999-12-22 2001-06-28 Aventis Pasteur Limited Chlamydia antigens and corresponding dna fragments and uses thereof
US7473531B1 (en) * 2003-08-08 2009-01-06 Colora Corporation Pancreatic cancer targets and uses thereof
US20100095387A1 (en) * 2005-07-15 2010-04-15 Martin Smith Methods and reagents for screening new drugs and for treating ion pump associated disorders and diseases
WO2010144611A2 (en) * 2009-06-10 2010-12-16 3-V Biosciences, Inc. Antivirals that target transporters, carriers, and ion channels
JP2014523884A (ja) * 2011-06-24 2014-09-18 セントローズ, エルエルシー 細胞外標的化薬物複合体
WO2014007868A2 (en) 2012-03-15 2014-01-09 The Regents Of The University Of California Low temperature sulfur and sodium metal battery for grid-scale energy storage application
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WO2017013648A1 (en) * 2015-07-19 2017-01-26 Yeda Research And Development Co. Ltd. SELECTIVE INHIBITORS OF Alpha2-CONTAINING ISOFORMS OF Na,K-ATPase AND USE THEREOF FOR REDUCTION OF INTRAOCULAR PRESSURE
JP7049249B2 (ja) * 2015-12-14 2022-04-06 コールド スプリング ハーバー ラボラトリー 中枢神経系疾患の処置のための組成物および方法
JP2020534788A (ja) * 2017-08-28 2020-12-03 ザ リージェンツ オブ ザ ユニバーシティ オブ カリフォルニア アデノ随伴ウイルスカプシド変異体及びその使用方法
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CN114072514A (zh) * 2019-05-14 2022-02-18 杜克大学 用于治疗atp酶介导的疾病的组合物和方法

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