JP2022541070A5 - - Google Patents

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Publication number
JP2022541070A5
JP2022541070A5 JP2022504139A JP2022504139A JP2022541070A5 JP 2022541070 A5 JP2022541070 A5 JP 2022541070A5 JP 2022504139 A JP2022504139 A JP 2022504139A JP 2022504139 A JP2022504139 A JP 2022504139A JP 2022541070 A5 JP2022541070 A5 JP 2022541070A5
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JP
Japan
Prior art keywords
nucleic acid
acid molecule
sequence
seq
exon
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Withdrawn
Application number
JP2022504139A
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English (en)
Japanese (ja)
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JP2022541070A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/IB2020/057038 external-priority patent/WO2021014428A1/en
Publication of JP2022541070A publication Critical patent/JP2022541070A/ja
Publication of JP2022541070A5 publication Critical patent/JP2022541070A5/ja
Priority to JP2025013522A priority Critical patent/JP2025069281A/ja
Withdrawn legal-status Critical Current

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JP2022504139A 2019-07-25 2020-07-24 調節可能な発現系 Withdrawn JP2022541070A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025013522A JP2025069281A (ja) 2019-07-25 2025-01-30 調節可能な発現系

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201962878514P 2019-07-25 2019-07-25
US62/878,514 2019-07-25
US202063013283P 2020-04-21 2020-04-21
US63/013,283 2020-04-21
PCT/IB2020/057038 WO2021014428A1 (en) 2019-07-25 2020-07-24 Regulatable expression systems

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025013522A Division JP2025069281A (ja) 2019-07-25 2025-01-30 調節可能な発現系

Publications (2)

Publication Number Publication Date
JP2022541070A JP2022541070A (ja) 2022-09-21
JP2022541070A5 true JP2022541070A5 (https=) 2023-08-01

Family

ID=71944162

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2022504139A Withdrawn JP2022541070A (ja) 2019-07-25 2020-07-24 調節可能な発現系
JP2025013522A Pending JP2025069281A (ja) 2019-07-25 2025-01-30 調節可能な発現系

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2025013522A Pending JP2025069281A (ja) 2019-07-25 2025-01-30 調節可能な発現系

Country Status (9)

Country Link
US (1) US20220307053A1 (https=)
EP (1) EP4004213A1 (https=)
JP (2) JP2022541070A (https=)
KR (1) KR20220035937A (https=)
CN (2) CN120137971A (https=)
AU (1) AU2020319168B2 (https=)
CA (1) CA3147574A1 (https=)
IL (1) IL289711A (https=)
WO (1) WO2021014428A1 (https=)

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CN115605596A (zh) * 2020-02-12 2023-01-13 费城儿童医院(Us) 用于基因表达的诱导型可变剪接调节的组合物和方法
US20240376493A1 (en) * 2021-04-21 2024-11-14 The Board Of Regents Of University Of Texas System Optimized ap4m1 polyneucleotides and expression cassettes and their use
GB2617565A (en) * 2022-04-11 2023-10-18 Ucl Business Ltd A construct, vector and system and uses thereof
WO2023219533A1 (ru) * 2022-05-11 2023-11-16 Общество С Ограниченной Ответственностью "Герофарм" Аденоассоциированный вирусный вектор на основе серотипа aav.php.b и его применение
WO2024060205A1 (zh) * 2022-09-23 2024-03-28 北京基驭医疗科技有限公司 包含基于小分子药物的可变剪接调节元件的核酸分子
GB202215198D0 (en) * 2022-10-14 2022-11-30 Univ Sheffield Gene therapy treatment
CN120826470A (zh) * 2023-03-06 2025-10-21 新加坡科技研究局 用于在哺乳动物细胞中共表达多基因的工程化弗林蛋白酶切割序列
WO2024216232A2 (en) * 2023-04-14 2024-10-17 Rgenta Therapeutics, Inc. Small-molecule regulated alternative splicing
WO2025015060A1 (en) * 2023-07-11 2025-01-16 Brave Bio, Inc. Engineered vectorized antibodies with reduced stability in systemic circulation and uses thereof

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