JP2025515030A5 - - Google Patents

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Publication number
JP2025515030A5
JP2025515030A5 JP2024564665A JP2024564665A JP2025515030A5 JP 2025515030 A5 JP2025515030 A5 JP 2025515030A5 JP 2024564665 A JP2024564665 A JP 2024564665A JP 2024564665 A JP2024564665 A JP 2024564665A JP 2025515030 A5 JP2025515030 A5 JP 2025515030A5
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JP
Japan
Application number
JP2024564665A
Other languages
Japanese (ja)
Other versions
JPWO2023213831A5 (https=
JP2025515030A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/EP2023/061582 external-priority patent/WO2023213831A1/en
Publication of JP2025515030A publication Critical patent/JP2025515030A/ja
Publication of JPWO2023213831A5 publication Critical patent/JPWO2023213831A5/ja
Publication of JP2025515030A5 publication Critical patent/JP2025515030A5/ja
Pending legal-status Critical Current

Links

JP2024564665A 2022-05-02 2023-05-02 遺伝子編集用の相同性非依存性標的組込み Pending JP2025515030A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
EP22171218.5 2022-05-02
EP22171218 2022-05-02
PCT/EP2023/061582 WO2023213831A1 (en) 2022-05-02 2023-05-02 Homology independent targeted integration for gene editing

Publications (3)

Publication Number Publication Date
JP2025515030A JP2025515030A (ja) 2025-05-13
JPWO2023213831A5 JPWO2023213831A5 (https=) 2026-03-19
JP2025515030A5 true JP2025515030A5 (https=) 2026-03-19

Family

ID=82218344

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024564665A Pending JP2025515030A (ja) 2022-05-02 2023-05-02 遺伝子編集用の相同性非依存性標的組込み

Country Status (8)

Country Link
US (1) US20250288694A1 (https=)
EP (1) EP4518907A1 (https=)
JP (1) JP2025515030A (https=)
CN (1) CN119136844A (https=)
AU (1) AU2023264251A1 (https=)
CA (1) CA3250913A1 (https=)
IL (1) IL316555A (https=)
WO (1) WO2023213831A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025229995A1 (ja) * 2024-04-30 2025-11-06 学校法人自治医科大学 核酸導入用ベクター、核酸導入方法、ポリヌクレオチド、及びベクター

Family Cites Families (21)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6933A (en) 1849-12-11 Brick-press
US113A (en) 1837-01-31 Improvement in the mode of making or preparing door-plates
GB9710809D0 (en) 1997-05-23 1997-07-23 Medical Res Council Nucleic acid binding proteins
DE69942334D1 (de) 1998-03-02 2010-06-17 Massachusetts Inst Technology Poly-zinkfinger-proteine mit verbesserten linkern
US6534261B1 (en) 1999-01-12 2003-03-18 Sangamo Biosciences, Inc. Regulation of endogenous gene expression in cells using zinc finger proteins
US7013219B2 (en) 1999-01-12 2006-03-14 Sangamo Biosciences, Inc. Regulation of endogenous gene expression in cells using zinc finger proteins
US7030215B2 (en) 1999-03-24 2006-04-18 Sangamo Biosciences, Inc. Position dependent recognition of GNN nucleotide triplets by zinc fingers
US20030104526A1 (en) 1999-03-24 2003-06-05 Qiang Liu Position dependent recognition of GNN nucleotide triplets by zinc fingers
US6794136B1 (en) 2000-11-20 2004-09-21 Sangamo Biosciences, Inc. Iterative optimization in the design of binding proteins
WO2003059396A1 (en) 2002-01-11 2003-07-24 Sergei Zolotukhin Adiponectin gene therapy
US20030232410A1 (en) 2002-03-21 2003-12-18 Monika Liljedahl Methods and compositions for using zinc finger endonucleases to enhance homologous recombination
WO2006036465A2 (en) 2004-09-03 2006-04-06 University Of Florida Compositions and methods for treating cystic fibrosis
US20090203140A1 (en) 2007-09-27 2009-08-13 Sangamo Biosciences, Inc. Genomic editing in zebrafish using zinc finger nucleases
HUE041436T2 (hu) 2009-12-10 2019-05-28 Univ Minnesota Tal-effektor-közvetített DNS-módosítás
EP3241902B1 (en) 2012-05-25 2018-02-28 The Regents of The University of California Methods and compositions for rna-directed target dna modification and for rna-directed modulation of transcription
DK3444342T3 (da) * 2012-07-11 2020-08-24 Sangamo Therapeutics Inc Fremgangsmåder og sammensætninger til behandlingen af lysosomale aflejringssygdomme
WO2018013932A1 (en) * 2016-07-15 2018-01-18 Salk Institute For Biological Studies Methods and compositions for genome editing in non-dividing cells
EP3867375A1 (en) 2018-10-15 2021-08-25 Fondazione Telethon Genome editing methods and constructs
WO2020206162A1 (en) * 2019-04-03 2020-10-08 Regeneron Pharmaceuticals, Inc. Methods and compositions for insertion of antibody coding sequences into a safe harbor locus
CN113058041B (zh) * 2020-08-27 2022-04-05 华东师范大学 一种用于治疗庞贝氏病的产品
CN112741906B (zh) * 2019-10-31 2022-07-05 华东师范大学 一种用于治疗b型血友病的产品

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