JP2025515030A5 - - Google Patents
Info
- Publication number
- JP2025515030A5 JP2025515030A5 JP2024564665A JP2024564665A JP2025515030A5 JP 2025515030 A5 JP2025515030 A5 JP 2025515030A5 JP 2024564665 A JP2024564665 A JP 2024564665A JP 2024564665 A JP2024564665 A JP 2024564665A JP 2025515030 A5 JP2025515030 A5 JP 2025515030A5
- Authority
- JP
- Japan
- Prior art keywords
- sequence
- nucleic acid
- nuclease
- target sequence
- cells
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| EP22171218.5 | 2022-05-02 | ||
| EP22171218 | 2022-05-02 | ||
| PCT/EP2023/061582 WO2023213831A1 (en) | 2022-05-02 | 2023-05-02 | Homology independent targeted integration for gene editing |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2025515030A JP2025515030A (ja) | 2025-05-13 |
| JP2025515030A5 true JP2025515030A5 (https=) | 2026-03-19 |
Family
ID=82218344
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024564665A Pending JP2025515030A (ja) | 2022-05-02 | 2023-05-02 | 遺伝子編集用の相同性非依存性標的組込み |
Country Status (8)
| Country | Link |
|---|---|
| US (1) | US20250288694A1 (https=) |
| EP (1) | EP4518907A1 (https=) |
| JP (1) | JP2025515030A (https=) |
| CN (1) | CN119136844A (https=) |
| AU (1) | AU2023264251A1 (https=) |
| CA (1) | CA3250913A1 (https=) |
| IL (1) | IL316555A (https=) |
| WO (1) | WO2023213831A1 (https=) |
Families Citing this family (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2025229995A1 (ja) * | 2024-04-30 | 2025-11-06 | 学校法人自治医科大学 | 核酸導入用ベクター、核酸導入方法、ポリヌクレオチド、及びベクター |
Family Cites Families (21)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US113A (en) | 1837-01-31 | Improvement in the mode of making or preparing door-plates | ||
| US6933A (en) | 1849-12-11 | Brick-press | ||
| GB9710809D0 (en) | 1997-05-23 | 1997-07-23 | Medical Res Council | Nucleic acid binding proteins |
| ES2341926T3 (es) | 1998-03-02 | 2010-06-29 | Massachusetts Institute Of Technology | Poliproteinas con dedos de cinc que tienen enlazadores mejorados. |
| US6534261B1 (en) | 1999-01-12 | 2003-03-18 | Sangamo Biosciences, Inc. | Regulation of endogenous gene expression in cells using zinc finger proteins |
| US7013219B2 (en) | 1999-01-12 | 2006-03-14 | Sangamo Biosciences, Inc. | Regulation of endogenous gene expression in cells using zinc finger proteins |
| US20030104526A1 (en) | 1999-03-24 | 2003-06-05 | Qiang Liu | Position dependent recognition of GNN nucleotide triplets by zinc fingers |
| US7030215B2 (en) | 1999-03-24 | 2006-04-18 | Sangamo Biosciences, Inc. | Position dependent recognition of GNN nucleotide triplets by zinc fingers |
| US6794136B1 (en) | 2000-11-20 | 2004-09-21 | Sangamo Biosciences, Inc. | Iterative optimization in the design of binding proteins |
| WO2003059396A1 (en) | 2002-01-11 | 2003-07-24 | Sergei Zolotukhin | Adiponectin gene therapy |
| WO2003080809A2 (en) | 2002-03-21 | 2003-10-02 | Sangamo Biosciences, Inc. | Methods and compositions for using zinc finger endonucleases to enhance homologous recombination |
| WO2006036465A2 (en) | 2004-09-03 | 2006-04-06 | University Of Florida | Compositions and methods for treating cystic fibrosis |
| AU2008305590A1 (en) | 2007-09-27 | 2009-04-02 | Sangamo Therapeutics, Inc. | Genomic editing in zebrafish using zinc finger nucleases |
| WO2011072246A2 (en) | 2009-12-10 | 2011-06-16 | Regents Of The University Of Minnesota | Tal effector-mediated dna modification |
| AU2013266968B2 (en) | 2012-05-25 | 2017-06-29 | Emmanuelle CHARPENTIER | Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription |
| EP3196301B1 (en) * | 2012-07-11 | 2018-10-17 | Sangamo Therapeutics, Inc. | Methods and compositions for the treatment of monogenic diseases |
| EP4321623A3 (en) * | 2016-07-15 | 2024-05-15 | Salk Institute for Biological Studies | Methods and compositions for genome editing in non-dividing cells |
| JP2022505139A (ja) | 2018-10-15 | 2022-01-14 | フォンダッツィオーネ・テレソン | ゲノム編集の方法及び構築物 |
| AU2020256225B9 (en) * | 2019-04-03 | 2025-04-10 | Regeneron Pharmaceuticals, Inc. | Methods and compositions for insertion of antibody coding sequences into a safe harbor locus |
| CN113058041B (zh) * | 2020-08-27 | 2022-04-05 | 华东师范大学 | 一种用于治疗庞贝氏病的产品 |
| CN112741906B (zh) * | 2019-10-31 | 2022-07-05 | 华东师范大学 | 一种用于治疗b型血友病的产品 |
-
2023
- 2023-05-02 EP EP23724720.0A patent/EP4518907A1/en active Pending
- 2023-05-02 CA CA3250913A patent/CA3250913A1/en active Pending
- 2023-05-02 JP JP2024564665A patent/JP2025515030A/ja active Pending
- 2023-05-02 US US18/862,191 patent/US20250288694A1/en active Pending
- 2023-05-02 WO PCT/EP2023/061582 patent/WO2023213831A1/en not_active Ceased
- 2023-05-02 IL IL316555A patent/IL316555A/en unknown
- 2023-05-02 AU AU2023264251A patent/AU2023264251A1/en active Pending
- 2023-05-02 CN CN202380038162.1A patent/CN119136844A/zh active Pending
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