JP2025515356A5 - - Google Patents
Info
- Publication number
- JP2025515356A5 JP2025515356A5 JP2024563591A JP2024563591A JP2025515356A5 JP 2025515356 A5 JP2025515356 A5 JP 2025515356A5 JP 2024563591 A JP2024563591 A JP 2024563591A JP 2024563591 A JP2024563591 A JP 2024563591A JP 2025515356 A5 JP2025515356 A5 JP 2025515356A5
- Authority
- JP
- Japan
- Prior art keywords
- aav
- nucleic acid
- raav
- bdd
- fviii
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| RU2022111695 | 2022-04-28 | ||
| RU2022111695A RU2818229C2 (ru) | 2022-04-28 | Выделенная нуклеиновая кислота, которая кодирует слитый белок на основе FVIII-BDD и гетерологичного сигнального пептида, и ее применение | |
| PCT/RU2023/050093 WO2023211315A1 (en) | 2022-04-28 | 2023-04-18 | Isolated nucleic acid that encodes fusion protein based on fviii-bdd and on heterologous signal peptide |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2025515356A JP2025515356A (ja) | 2025-05-14 |
| JP2025515356A5 true JP2025515356A5 (https=) | 2026-04-28 |
Family
ID=88519415
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024563591A Pending JP2025515356A (ja) | 2022-04-28 | 2023-04-18 | Fviii-bddおよび異種シグナルペプチドに基づく融合タンパク質をコードする単離された核酸 |
Country Status (19)
| Country | Link |
|---|---|
| EP (1) | EP4514975A1 (https=) |
| JP (1) | JP2025515356A (https=) |
| KR (1) | KR20250005425A (https=) |
| CN (1) | CN117402901A (https=) |
| AR (1) | AR129164A1 (https=) |
| AU (1) | AU2023261711A1 (https=) |
| CA (1) | CA3250663A1 (https=) |
| CL (1) | CL2024003295A1 (https=) |
| CO (1) | CO2024014703A2 (https=) |
| CR (1) | CR20240525A (https=) |
| IL (1) | IL316578A (https=) |
| JO (1) | JOP20240240A1 (https=) |
| MA (1) | MA68435A1 (https=) |
| MX (1) | MX2024013281A (https=) |
| PE (1) | PE20251064A1 (https=) |
| PY (1) | PY2331055A (https=) |
| TW (1) | TW202342751A (https=) |
| UY (1) | UY40243A (https=) |
| WO (1) | WO2023211315A1 (https=) |
Families Citing this family (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN120365434A (zh) * | 2024-01-23 | 2025-07-25 | 上海苹谱医疗科技有限公司 | 一种提高凝血因子ⅷ分泌水平的双信号肽及其应用 |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| PL3326643T3 (pl) * | 2009-12-06 | 2021-10-25 | Bioverativ Therapeutics Inc. | Chimeryczne i hybrydowe polipeptydy czynnika VIII-FC oraz sposoby ich zastosowania |
| JP2016519110A (ja) * | 2013-04-22 | 2016-06-30 | キャタレント ファーマ ソリューションズ リミテッド ライアビリティ カンパニー | 獣医学的デコリン組成物及びそれらの使用 |
| RU2647769C2 (ru) * | 2015-12-30 | 2018-03-19 | Закрытое Акционерное Общество "Биокад" | Химерный улучшенный рекомбинантный фактор VIII |
| WO2017136358A1 (en) * | 2016-02-01 | 2017-08-10 | Bioverativ Therapeutics Inc. | Optimized factor viii genes |
| CN114651065B (zh) * | 2019-09-03 | 2024-08-20 | 五松尖端医疗产业振兴财团 | 导入用于提高蛋白质生产性的单个条形码系统的信号肽超高速筛选方法 |
| EP4051704A2 (en) * | 2019-11-01 | 2022-09-07 | Freeline Therapeutics Limited | Factor viii construct |
-
2023
- 2023-04-18 AU AU2023261711A patent/AU2023261711A1/en active Pending
- 2023-04-18 IL IL316578A patent/IL316578A/en unknown
- 2023-04-18 KR KR1020247039725A patent/KR20250005425A/ko active Pending
- 2023-04-18 JP JP2024563591A patent/JP2025515356A/ja active Pending
- 2023-04-18 EP EP23796915.9A patent/EP4514975A1/en active Pending
- 2023-04-18 CA CA3250663A patent/CA3250663A1/en active Pending
- 2023-04-18 MA MA68435A patent/MA68435A1/fr unknown
- 2023-04-18 CR CR20240525A patent/CR20240525A/es unknown
- 2023-04-18 PE PE2024002341A patent/PE20251064A1/es unknown
- 2023-04-18 WO PCT/RU2023/050093 patent/WO2023211315A1/en not_active Ceased
- 2023-04-19 TW TW112114536A patent/TW202342751A/zh unknown
- 2023-04-26 UY UY0001040243A patent/UY40243A/es unknown
- 2023-04-27 PY PY202302331055A patent/PY2331055A/es unknown
- 2023-04-27 AR ARP230101023A patent/AR129164A1/es unknown
- 2023-04-27 CN CN202310468986.4A patent/CN117402901A/zh active Pending
-
2024
- 2024-10-27 JO JOJO/P/2024/0240A patent/JOP20240240A1/ar unknown
- 2024-10-28 MX MX2024013281A patent/MX2024013281A/es unknown
- 2024-10-28 CL CL2024003295A patent/CL2024003295A1/es unknown
- 2024-10-28 CO CONC2024/0014703A patent/CO2024014703A2/es unknown
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| JP2024009857A5 (https=) | ||
| US20210147875A1 (en) | Compositions for targeting conducting airway cells comprising adeno-associated virus constructs | |
| JP2021087431A5 (https=) | ||
| JP2021019591A5 (https=) | ||
| JP2019116492A5 (https=) | ||
| JP2021523718A5 (https=) | ||
| RU2021102893A (ru) | Модифицированные гены атаксии фридрейха и векторы для генной терапии | |
| JPWO2020106916A5 (https=) | ||
| JP2007507223A5 (https=) | ||
| JPWO2021077000A5 (https=) | ||
| JP2021520811A5 (https=) | ||
| CN121925426A (zh) | 肝脏去靶向衣壳 | |
| JP2021534766A5 (https=) | ||
| CN120787264A (zh) | 肝脏去靶向衣壳 | |
| JP2025515356A5 (https=) | ||
| JPWO2019165050A5 (https=) | ||
| JPWO2021050614A5 (https=) | ||
| JP2020510433A5 (https=) | ||
| JP2025516136A5 (https=) | ||
| JP2021521782A5 (https=) | ||
| JPWO2021163556A5 (https=) | ||
| JPWO2022036220A5 (https=) | ||
| JPWO2021108809A5 (https=) | ||
| JPWO2021014428A5 (https=) | ||
| JP2025514313A5 (https=) |