JP2025515356A5 - - Google Patents

Info

Publication number
JP2025515356A5
JP2025515356A5 JP2024563591A JP2024563591A JP2025515356A5 JP 2025515356 A5 JP2025515356 A5 JP 2025515356A5 JP 2024563591 A JP2024563591 A JP 2024563591A JP 2024563591 A JP2024563591 A JP 2024563591A JP 2025515356 A5 JP2025515356 A5 JP 2025515356A5
Authority
JP
Japan
Prior art keywords
aav
nucleic acid
raav
bdd
fviii
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024563591A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025515356A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/RU2023/050093 external-priority patent/WO2023211315A1/en
Publication of JP2025515356A publication Critical patent/JP2025515356A/ja
Publication of JP2025515356A5 publication Critical patent/JP2025515356A5/ja
Pending legal-status Critical Current

Links

JP2024563591A 2022-04-28 2023-04-18 Fviii-bddおよび異種シグナルペプチドに基づく融合タンパク質をコードする単離された核酸 Pending JP2025515356A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
RU2022111695 2022-04-28
RU2022111695A RU2818229C2 (ru) 2022-04-28 Выделенная нуклеиновая кислота, которая кодирует слитый белок на основе FVIII-BDD и гетерологичного сигнального пептида, и ее применение
PCT/RU2023/050093 WO2023211315A1 (en) 2022-04-28 2023-04-18 Isolated nucleic acid that encodes fusion protein based on fviii-bdd and on heterologous signal peptide

Publications (2)

Publication Number Publication Date
JP2025515356A JP2025515356A (ja) 2025-05-14
JP2025515356A5 true JP2025515356A5 (https=) 2026-04-28

Family

ID=88519415

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024563591A Pending JP2025515356A (ja) 2022-04-28 2023-04-18 Fviii-bddおよび異種シグナルペプチドに基づく融合タンパク質をコードする単離された核酸

Country Status (19)

Country Link
EP (1) EP4514975A1 (https=)
JP (1) JP2025515356A (https=)
KR (1) KR20250005425A (https=)
CN (1) CN117402901A (https=)
AR (1) AR129164A1 (https=)
AU (1) AU2023261711A1 (https=)
CA (1) CA3250663A1 (https=)
CL (1) CL2024003295A1 (https=)
CO (1) CO2024014703A2 (https=)
CR (1) CR20240525A (https=)
IL (1) IL316578A (https=)
JO (1) JOP20240240A1 (https=)
MA (1) MA68435A1 (https=)
MX (1) MX2024013281A (https=)
PE (1) PE20251064A1 (https=)
PY (1) PY2331055A (https=)
TW (1) TW202342751A (https=)
UY (1) UY40243A (https=)
WO (1) WO2023211315A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN120365434A (zh) * 2024-01-23 2025-07-25 上海苹谱医疗科技有限公司 一种提高凝血因子ⅷ分泌水平的双信号肽及其应用

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
PL3326643T3 (pl) * 2009-12-06 2021-10-25 Bioverativ Therapeutics Inc. Chimeryczne i hybrydowe polipeptydy czynnika VIII-FC oraz sposoby ich zastosowania
JP2016519110A (ja) * 2013-04-22 2016-06-30 キャタレント ファーマ ソリューションズ リミテッド ライアビリティ カンパニー 獣医学的デコリン組成物及びそれらの使用
RU2647769C2 (ru) * 2015-12-30 2018-03-19 Закрытое Акционерное Общество "Биокад" Химерный улучшенный рекомбинантный фактор VIII
WO2017136358A1 (en) * 2016-02-01 2017-08-10 Bioverativ Therapeutics Inc. Optimized factor viii genes
CN114651065B (zh) * 2019-09-03 2024-08-20 五松尖端医疗产业振兴财团 导入用于提高蛋白质生产性的单个条形码系统的信号肽超高速筛选方法
EP4051704A2 (en) * 2019-11-01 2022-09-07 Freeline Therapeutics Limited Factor viii construct

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