JP2023541443A5 - - Google Patents
Info
- Publication number
- JP2023541443A5 JP2023541443A5 JP2023516689A JP2023516689A JP2023541443A5 JP 2023541443 A5 JP2023541443 A5 JP 2023541443A5 JP 2023516689 A JP2023516689 A JP 2023516689A JP 2023516689 A JP2023516689 A JP 2023516689A JP 2023541443 A5 JP2023541443 A5 JP 2023541443A5
- Authority
- JP
- Japan
- Prior art keywords
- gjb2
- nucleic acid
- optionally
- cells
- isolated nucleic
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063078233P | 2020-09-14 | 2020-09-14 | |
| US63/078,233 | 2020-09-14 | ||
| US202163161619P | 2021-03-16 | 2021-03-16 | |
| US63/161,619 | 2021-03-16 | ||
| PCT/US2021/050205 WO2022056444A1 (en) | 2020-09-14 | 2021-09-14 | Recombinant adeno associated virus (raav) encoding gjb2 and uses thereof |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023541443A JP2023541443A (ja) | 2023-10-02 |
| JP2023541443A5 true JP2023541443A5 (https=) | 2024-09-26 |
Family
ID=80631939
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023516689A Pending JP2023541443A (ja) | 2020-09-14 | 2021-09-14 | ＧＪＢ２をコードする組換えアデノ随伴ウイルス（ｒＡＡＶ）およびその使用。 |
Country Status (10)
| Country | Link |
|---|---|
| EP (1) | EP4211151A4 (https=) |
| JP (1) | JP2023541443A (https=) |
| KR (1) | KR20230069157A (https=) |
| AU (1) | AU2021339843A1 (https=) |
| BR (1) | BR112023004605A2 (https=) |
| CA (1) | CA3191533A1 (https=) |
| IL (1) | IL301057A (https=) |
| MX (1) | MX2023002978A (https=) |
| TW (1) | TW202227476A (https=) |
| WO (1) | WO2022056444A1 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2021067448A1 (en) * | 2019-09-30 | 2021-04-08 | Applied Genetic Technologies Corporation | Adeno-associated virus (aav) systems for treatment of genetic hearing loss |
| WO2024011224A2 (en) * | 2022-07-08 | 2024-01-11 | The Trustees Of Columbia University In The City Of New York | Regulatory element for cell type specific expression of genes in spinal motor neurons |
| WO2024218192A1 (en) * | 2023-04-18 | 2024-10-24 | Uniqure Biopharma B.V. | Novel neurotropic adeno-associated virus capsids with detargeting of peripheral organs |
| EP4713463A1 (en) * | 2023-05-18 | 2026-03-25 | Decibel Therapeutics, Inc. | Compositions and methods for treating gjb2-related hearing loss |
Family Cites Families (9)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP1308458A1 (en) * | 2001-10-30 | 2003-05-07 | GenOdyssee | New polynucleotides and polypeptides of the CX26 gene |
| DE602005019174D1 (de) * | 2004-06-17 | 2010-03-18 | Epigenomics Ag | Zusammensetzungen und verfahren zur verhinderung des mitschleppens einer kontamination in nukleinsäure-amplifikationsreaktionen |
| CN101389769A (zh) * | 2005-12-28 | 2009-03-18 | 森托科尔公司 | 用于评价和治疗银屑病及相关疾病的标记与方法 |
| WO2019200016A1 (en) * | 2018-04-10 | 2019-10-17 | President And Fellows Of Harvard College | Aav vectors encoding clarin-1 or gjb2 and uses thereof |
| WO2020077295A1 (en) * | 2018-10-11 | 2020-04-16 | Decibel Therapeutics, Inc. | Aav1 vectors and uses thereof for treatment of otic indications |
| EP4063510A1 (en) * | 2018-11-07 | 2022-09-28 | Akouos, Inc. | Use of adeno-associated viral vectors to correct gene defects/ express proteins in hair cells and supporting cells in the inner ear |
| WO2021067448A1 (en) * | 2019-09-30 | 2021-04-08 | Applied Genetic Technologies Corporation | Adeno-associated virus (aav) systems for treatment of genetic hearing loss |
| WO2021231808A2 (en) * | 2020-05-13 | 2021-11-18 | Akouos, Inc. | Compositions and methods for treating gjb2-associated hearing loss |
| MX2023013394A (es) * | 2021-05-13 | 2023-12-14 | Akouos Inc | Composiciones de suministro de terapia genica y metodos para tratar perdida auditiva. |
-
2021
- 2021-09-14 TW TW110134291A patent/TW202227476A/zh unknown
- 2021-09-14 JP JP2023516689A patent/JP2023541443A/ja active Pending
- 2021-09-14 IL IL301057A patent/IL301057A/en unknown
- 2021-09-14 EP EP21867807.6A patent/EP4211151A4/en active Pending
- 2021-09-14 MX MX2023002978A patent/MX2023002978A/es unknown
- 2021-09-14 BR BR112023004605A patent/BR112023004605A2/pt unknown
- 2021-09-14 WO PCT/US2021/050205 patent/WO2022056444A1/en not_active Ceased
- 2021-09-14 CA CA3191533A patent/CA3191533A1/en active Pending
- 2021-09-14 AU AU2021339843A patent/AU2021339843A1/en active Pending
- 2021-09-14 KR KR1020237012321A patent/KR20230069157A/ko active Pending
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