JP2022527126A5 - - Google Patents

Info

Publication number
JP2022527126A5
JP2022527126A5 JP2021560050A JP2021560050A JP2022527126A5 JP 2022527126 A5 JP2022527126 A5 JP 2022527126A5 JP 2021560050 A JP2021560050 A JP 2021560050A JP 2021560050 A JP2021560050 A JP 2021560050A JP 2022527126 A5 JP2022527126 A5 JP 2022527126A5
Authority
JP
Japan
Prior art keywords
nucleic acid
isolated nucleic
sequence
seq
acid according
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2021560050A
Other languages
English (en)
Japanese (ja)
Other versions
JP2022527126A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/027452 external-priority patent/WO2020210480A2/en
Publication of JP2022527126A publication Critical patent/JP2022527126A/ja
Publication of JP2022527126A5 publication Critical patent/JP2022527126A5/ja
Pending legal-status Critical Current

Links

JP2021560050A 2019-04-10 2020-04-09 H因子ベクターおよびその使用 Pending JP2022527126A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962831870P 2019-04-10 2019-04-10
US62/831,870 2019-04-10
PCT/US2020/027452 WO2020210480A2 (en) 2019-04-10 2020-04-09 Factor h vectors and uses thereof

Publications (2)

Publication Number Publication Date
JP2022527126A JP2022527126A (ja) 2022-05-30
JP2022527126A5 true JP2022527126A5 (https=) 2023-04-18

Family

ID=72750649

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2021560050A Pending JP2022527126A (ja) 2019-04-10 2020-04-09 H因子ベクターおよびその使用

Country Status (10)

Country Link
US (1) US12570997B2 (https=)
EP (1) EP3966231A4 (https=)
JP (1) JP2022527126A (https=)
KR (1) KR20210149803A (https=)
CN (1) CN113924313A (https=)
AU (1) AU2020272875A1 (https=)
BR (1) BR112021019032A2 (https=)
CA (1) CA3135367A1 (https=)
IL (1) IL287071A (https=)
WO (1) WO2020210480A2 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN108291216B (zh) 2015-09-24 2022-09-16 宾夕法尼亚州大学信托人 用于治疗补体介导的疾病的组合物和方法
US20250205365A1 (en) * 2022-03-18 2025-06-26 University Of Florida Research Foundation, Incorporated Methods and compositions for treating rbm20 related cardiomyopathy with a viral vector

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP2561073B1 (en) 2010-04-23 2016-08-24 University of Massachusetts Cns targeting aav vectors and methods of use thereof
CA2920293A1 (en) 2013-08-16 2015-02-19 Alexion Pharmaceuticals, Inc. Treatment of graft rejection by administering a complement inhibitor to an organ prior to transplant
WO2017019876A1 (en) * 2015-07-28 2017-02-02 University Of Massachusetts Transgenic expression of dnase i in vivo delivered by an adeno-associated virus vector
WO2017024198A1 (en) * 2015-08-06 2017-02-09 The Trustees Of The University Of Pennsylvania Glp-1 and use thereof in compositions for treating metabolic diseases
CN108291216B (zh) * 2015-09-24 2022-09-16 宾夕法尼亚州大学信托人 用于治疗补体介导的疾病的组合物和方法
KR20190088561A (ko) * 2016-12-07 2019-07-26 유니버시티 오브 플로리다 리서치 파운데이션, 인코포레이티드 인터류킨-1 수용체 길항제(IL-1RA) cDNA

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