JP2024506266A5 - - Google Patents
Info
- Publication number
- JP2024506266A5 JP2024506266A5 JP2023545212A JP2023545212A JP2024506266A5 JP 2024506266 A5 JP2024506266 A5 JP 2024506266A5 JP 2023545212 A JP2023545212 A JP 2023545212A JP 2023545212 A JP2023545212 A JP 2023545212A JP 2024506266 A5 JP2024506266 A5 JP 2024506266A5
- Authority
- JP
- Japan
- Prior art keywords
- sequence
- seq
- polynucleotide
- signal peptide
- inhibitor
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Withdrawn
Links
Applications Claiming Priority (7)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163142121P | 2021-01-27 | 2021-01-27 | |
| US63/142,121 | 2021-01-27 | ||
| US202163201466P | 2021-04-30 | 2021-04-30 | |
| US63/201,466 | 2021-04-30 | ||
| US202163261603P | 2021-09-24 | 2021-09-24 | |
| US63/261,603 | 2021-09-24 | ||
| PCT/US2022/014091 WO2022165027A2 (en) | 2021-01-27 | 2022-01-27 | Compositions and methods for treating hereditary angioedema |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024506266A JP2024506266A (ja) | 2024-02-13 |
| JP2024506266A5 true JP2024506266A5 (https=) | 2025-01-30 |
Family
ID=82653909
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023545212A Withdrawn JP2024506266A (ja) | 2021-01-27 | 2022-01-27 | 遺伝性血管性浮腫を治療するための組成物および方法 |
Country Status (12)
| Country | Link |
|---|---|
| US (1) | US20240110201A1 (https=) |
| EP (1) | EP4284417A4 (https=) |
| JP (1) | JP2024506266A (https=) |
| KR (1) | KR20230136147A (https=) |
| AU (1) | AU2022214192A1 (https=) |
| CA (1) | CA3207268A1 (https=) |
| CL (1) | CL2023002138A1 (https=) |
| CO (1) | CO2023011154A2 (https=) |
| IL (1) | IL304404A (https=) |
| MX (1) | MX2023008801A (https=) |
| PE (1) | PE20240692A1 (https=) |
| WO (1) | WO2022165027A2 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20240408240A1 (en) * | 2021-10-01 | 2024-12-12 | Biomarin Pharmaceutical Inc. | Treatment of hereditary angioedema with aav gene therapy vectors and therapeutic formulations |
| CN117947040A (zh) * | 2022-10-31 | 2024-04-30 | 苏州荷光科汇生物科技有限公司 | 用于目的基因的表达盒及其应用 |
| AU2024257493A1 (en) * | 2023-04-18 | 2025-12-04 | Siren Biotechnology, Inc. | Adeno-associated viral vector compositions and methods of use |
| WO2025110984A1 (en) * | 2023-11-21 | 2025-05-30 | Hydrogene Therapeutics, Inc. | Compositions and methods for treating wilson's disease |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| KR101610268B1 (ko) * | 2007-08-28 | 2016-04-07 | 애들레이드 리서치 앤드 이노베이션 피티와이 리미티드 | 외과용 하이드로겔 |
| WO2013151665A2 (en) * | 2012-04-02 | 2013-10-10 | modeRNA Therapeutics | Modified polynucleotides for the production of proteins associated with human disease |
| CN108064176A (zh) * | 2015-04-22 | 2018-05-22 | 库瑞瓦格股份公司 | 用于治疗肿瘤疾病的含有rna的组合物 |
| US10214731B2 (en) * | 2015-05-28 | 2019-02-26 | Cornell University | Adeno-associated virus mediated delivery of C1E1 as a therapy for angioedema |
| WO2021081280A1 (en) * | 2019-10-23 | 2021-04-29 | Shire Human Genetic Therapies, Inc. | Adeno-associated virus vectors based gene therapy for hereditary angioedema |
| JP2023503850A (ja) * | 2019-11-14 | 2023-02-01 | バイオマリン ファーマシューティカル インコーポレイテッド | 肝臓特異的遺伝子療法ベクターによる遺伝性血管浮腫の治療 |
-
2022
- 2022-01-27 CA CA3207268A patent/CA3207268A1/en active Pending
- 2022-01-27 JP JP2023545212A patent/JP2024506266A/ja not_active Withdrawn
- 2022-01-27 AU AU2022214192A patent/AU2022214192A1/en not_active Abandoned
- 2022-01-27 PE PE2023002174A patent/PE20240692A1/es unknown
- 2022-01-27 WO PCT/US2022/014091 patent/WO2022165027A2/en not_active Ceased
- 2022-01-27 EP EP22746602.6A patent/EP4284417A4/en not_active Withdrawn
- 2022-01-27 MX MX2023008801A patent/MX2023008801A/es unknown
- 2022-01-27 KR KR1020237028214A patent/KR20230136147A/ko active Pending
- 2022-01-27 US US18/262,959 patent/US20240110201A1/en active Pending
-
2023
- 2023-07-11 IL IL304404A patent/IL304404A/en unknown
- 2023-07-21 CL CL2023002138A patent/CL2023002138A1/es unknown
- 2023-08-25 CO CONC2023/0011154A patent/CO2023011154A2/es unknown