JP2020520643A5 - - Google Patents
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- Publication number
- JP2020520643A5 JP2020520643A5 JP2019563548A JP2019563548A JP2020520643A5 JP 2020520643 A5 JP2020520643 A5 JP 2020520643A5 JP 2019563548 A JP2019563548 A JP 2019563548A JP 2019563548 A JP2019563548 A JP 2019563548A JP 2020520643 A5 JP2020520643 A5 JP 2020520643A5
- Authority
- JP
- Japan
- Prior art keywords
- item
- expression cassette
- factor
- transgene
- cassette according
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (2)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2022152422A JP2022173348A (ja) | 2017-05-19 | 2022-09-26 | 高活性制御エレメント |
| JP2023211093A JP2024015408A (ja) | 2017-05-19 | 2023-12-14 | 高活性制御エレメント |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201762508968P | 2017-05-19 | 2017-05-19 | |
| US62/508,968 | 2017-05-19 | ||
| PCT/US2018/033515 WO2018213786A1 (en) | 2017-05-19 | 2018-05-18 | High activity regulatory elements |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022152422A Division JP2022173348A (ja) | 2017-05-19 | 2022-09-26 | 高活性制御エレメント |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2020520643A JP2020520643A (ja) | 2020-07-16 |
| JP2020520643A5 true JP2020520643A5 (https=) | 2021-07-26 |
| JP7315475B2 JP7315475B2 (ja) | 2023-07-26 |
Family
ID=64274721
Family Applications (3)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019563548A Active JP7315475B2 (ja) | 2017-05-19 | 2018-05-18 | 高活性制御エレメント |
| JP2022152422A Pending JP2022173348A (ja) | 2017-05-19 | 2022-09-26 | 高活性制御エレメント |
| JP2023211093A Pending JP2024015408A (ja) | 2017-05-19 | 2023-12-14 | 高活性制御エレメント |
Family Applications After (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022152422A Pending JP2022173348A (ja) | 2017-05-19 | 2022-09-26 | 高活性制御エレメント |
| JP2023211093A Pending JP2024015408A (ja) | 2017-05-19 | 2023-12-14 | 高活性制御エレメント |
Country Status (11)
| Country | Link |
|---|---|
| US (2) | US12104175B2 (https=) |
| EP (1) | EP3624858A4 (https=) |
| JP (3) | JP7315475B2 (https=) |
| KR (2) | KR102636351B1 (https=) |
| CN (2) | CN110944674B (https=) |
| AU (1) | AU2018269050A1 (https=) |
| BR (1) | BR112019024222A2 (https=) |
| CA (1) | CA3063464A1 (https=) |
| MA (1) | MA49153A (https=) |
| TW (1) | TWI811219B (https=) |
| WO (1) | WO2018213786A1 (https=) |
Families Citing this family (16)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| GB201420139D0 (en) | 2014-11-12 | 2014-12-24 | Ucl Business Plc | Factor IX gene therapy |
| AU2018269050A1 (en) | 2017-05-19 | 2020-01-16 | Encoded Therapeutics, Inc. | High activity regulatory elements |
| EP3717505A4 (en) | 2017-12-01 | 2021-12-01 | Encoded Therapeutics, Inc. | GENENICALLY MODIFIED DNA-BINDING PROTEINS |
| US10842885B2 (en) | 2018-08-20 | 2020-11-24 | Ucl Business Ltd | Factor IX encoding nucleotides |
| GB201813528D0 (en) | 2018-08-20 | 2018-10-03 | Ucl Business Plc | Factor IX encoding nucleotides |
| MX2021008739A (es) * | 2019-01-24 | 2021-10-13 | Valorisation Hsj Lp | Secuencias reguladoras de la transcripción específicas de células y usos de estas. |
| EP3952924A4 (en) * | 2019-04-12 | 2023-05-24 | Encoded Therapeutics, Inc. | COMPOSITIONS AND METHODS OF ADMINISTRATION OF THERAPEUTIC PRODUCTS |
| PL3976798T3 (pl) | 2019-05-29 | 2026-04-07 | Encoded Therapeutics, Inc. | Kompozycje i sposoby selektywnej regulacji genów |
| JP7759311B2 (ja) | 2019-07-19 | 2025-10-23 | フラッグシップ パイオニアリング イノベーションズ シックス，エルエルシー | リコンビナーゼ組成物及び使用方法 |
| CN113088519B (zh) * | 2019-12-23 | 2024-02-02 | 苏州华毅乐健生物科技有限公司 | 一种分离的核酸分子及其应用 |
| JP2023514204A (ja) * | 2020-02-14 | 2023-04-05 | ウルトラジェニックス ファーマシューティカル インコーポレイテッド | Ｃｄｋｌ５欠損障害を処置するための遺伝子治療 |
| KR20230003569A (ko) * | 2020-04-27 | 2023-01-06 | 더 트러스티스 오브 더 유니버시티 오브 펜실베니아 | Cdkl5 결핍 장애 (cdd)의 치료에 유용한 조성물 |
| US20250041450A1 (en) * | 2021-08-05 | 2025-02-06 | Insmed Incorporated | Adeno-associated virus particles and methods of use thereof |
| JP2025533994A (ja) * | 2022-10-11 | 2025-10-09 | メイラグティーエックス ユーケー アイアイ リミティド | Ａｔｐ７ｂ遺伝子療法 |
| CN117925624B (zh) * | 2024-03-22 | 2024-05-31 | 上海凌医生物科技有限公司 | 一种金属响应调控元件 |
| CN117947035A (zh) * | 2024-03-25 | 2024-04-30 | 上海凌医生物科技有限公司 | 一种增强基因表达的启动子 |
Family Cites Families (13)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| ES2284545T3 (es) * | 1999-11-16 | 2007-11-16 | Genzyme Corporation | Vectores y transgenes con elementos reguladores para la administracion de genes del higado. |
| US6436703B1 (en) * | 2000-03-31 | 2002-08-20 | Hyseq, Inc. | Nucleic acids and polypeptides |
| EP1783645A1 (en) * | 2005-11-08 | 2007-05-09 | Actigenics | Methods for the identification of microRNA and their applications in research and human health |
| WO2008073303A2 (en) * | 2006-12-07 | 2008-06-19 | Switchgear Genomics | Transcriptional regulatory elements of biological pathways, tools, and methods |
| GB0911870D0 (en) | 2009-07-08 | 2009-08-19 | Ucl Business Plc | Optimised coding sequence and promoter |
| WO2013033627A2 (en) * | 2011-09-01 | 2013-03-07 | The Regents Of The University Of California | Diagnosis and treatment of arthritis using epigenetics |
| MX367100B (es) * | 2012-02-17 | 2019-08-05 | The Children´S Hospital Of Philadelphia | Composiciones del vector aav y metodos para su transferencia genetica a celulas, organos y tejidos. |
| ES2786051T3 (es) | 2012-10-25 | 2020-10-08 | Tocagen Inc | Vector retroviral con casete de mini-promotor |
| US11147887B2 (en) * | 2014-12-17 | 2021-10-19 | Fundación Para La Investigación Mèdica Aplicada | Nucleic acid constructs and gene therapy vectors for use in the treatment of Wilson disease |
| TWI707951B (zh) * | 2015-04-08 | 2020-10-21 | 美商健臻公司 | 過大腺相關載體之製造 |
| AU2018269050A1 (en) | 2017-05-19 | 2020-01-16 | Encoded Therapeutics, Inc. | High activity regulatory elements |
| EP3717505A4 (en) * | 2017-12-01 | 2021-12-01 | Encoded Therapeutics, Inc. | GENENICALLY MODIFIED DNA-BINDING PROTEINS |
| SG11202109362XA (en) * | 2019-02-28 | 2021-09-29 | Encoded Therapeutics Inc | Compositions and methods for treating laminopathies |
-
2018
- 2018-05-18 AU AU2018269050A patent/AU2018269050A1/en not_active Abandoned
- 2018-05-18 TW TW107117128A patent/TWI811219B/zh active
- 2018-05-18 JP JP2019563548A patent/JP7315475B2/ja active Active
- 2018-05-18 KR KR1020197037368A patent/KR102636351B1/ko active Active
- 2018-05-18 CA CA3063464A patent/CA3063464A1/en active Pending
- 2018-05-18 MA MA049153A patent/MA49153A/fr unknown
- 2018-05-18 CN CN201880048355.4A patent/CN110944674B/zh active Active
- 2018-05-18 CN CN202411101805.5A patent/CN118956965A/zh active Pending
- 2018-05-18 EP EP18803184.3A patent/EP3624858A4/en not_active Withdrawn
- 2018-05-18 WO PCT/US2018/033515 patent/WO2018213786A1/en not_active Ceased
- 2018-05-18 BR BR112019024222-8A patent/BR112019024222A2/pt not_active Application Discontinuation
- 2018-05-18 KR KR1020247004550A patent/KR20240024326A/ko not_active Ceased
-
2019
- 2019-11-18 US US16/687,426 patent/US12104175B2/en active Active
-
2022
- 2022-09-26 JP JP2022152422A patent/JP2022173348A/ja active Pending
-
2023
- 2023-12-14 JP JP2023211093A patent/JP2024015408A/ja active Pending
-
2024
- 2024-08-01 US US18/792,310 patent/US20240376441A1/en not_active Abandoned
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