JP2017513469A5 - - Google Patents

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JP2017513469A5
JP2017513469A5 JP2016560543A JP2016560543A JP2017513469A5 JP 2017513469 A5 JP2017513469 A5 JP 2017513469A5 JP 2016560543 A JP2016560543 A JP 2016560543A JP 2016560543 A JP2016560543 A JP 2016560543A JP 2017513469 A5 JP2017513469 A5 JP 2017513469A5
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modified
tds
sugar
internucleoside linkage
compound
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JP2016560543A
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JP6622214B2 (ja
JP2017513469A (ja
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Priority claimed from PCT/US2015/023934 external-priority patent/WO2015153800A2/en
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JP2016560543A 2014-04-01 2015-04-01 Sod−1発現を調節するための組成物 Active JP6622214B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201461973803P 2014-04-01 2014-04-01
US61/973,803 2014-04-01
PCT/US2015/023934 WO2015153800A2 (en) 2014-04-01 2015-04-01 Compositions for modulating sod-1 expression

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2019141933A Division JP2019201664A (ja) 2014-04-01 2019-08-01 Sod−1発現を調節するための組成物

Publications (3)

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JP2017513469A JP2017513469A (ja) 2017-06-01
JP2017513469A5 true JP2017513469A5 (OSRAM) 2018-06-14
JP6622214B2 JP6622214B2 (ja) 2019-12-18

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Application Number Title Priority Date Filing Date
JP2016560543A Active JP6622214B2 (ja) 2014-04-01 2015-04-01 Sod−1発現を調節するための組成物
JP2019141933A Withdrawn JP2019201664A (ja) 2014-04-01 2019-08-01 Sod−1発現を調節するための組成物
JP2021014429A Active JP7198298B2 (ja) 2014-04-01 2021-02-01 Sod-1発現を調節するための組成物
JP2022200959A Withdrawn JP2023027299A (ja) 2014-04-01 2022-12-16 Sod-1発現を調節するための組成物
JP2024085318A Pending JP2024105714A (ja) 2014-04-01 2024-05-27 Sod-1発現を調節するための組成物

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JP2019141933A Withdrawn JP2019201664A (ja) 2014-04-01 2019-08-01 Sod−1発現を調節するための組成物
JP2021014429A Active JP7198298B2 (ja) 2014-04-01 2021-02-01 Sod-1発現を調節するための組成物
JP2022200959A Withdrawn JP2023027299A (ja) 2014-04-01 2022-12-16 Sod-1発現を調節するための組成物
JP2024085318A Pending JP2024105714A (ja) 2014-04-01 2024-05-27 Sod-1発現を調節するための組成物

Country Status (30)

Country Link
US (3) US10385341B2 (OSRAM)
EP (3) EP4137573A3 (OSRAM)
JP (5) JP6622214B2 (OSRAM)
KR (6) KR20250113519A (OSRAM)
CN (2) CN111440798A (OSRAM)
AU (4) AU2015240761B2 (OSRAM)
BR (1) BR112016021848B1 (OSRAM)
CA (1) CA2942394A1 (OSRAM)
CL (3) CL2016002509A1 (OSRAM)
CY (1) CY1123288T1 (OSRAM)
DK (2) DK3757214T3 (OSRAM)
ES (2) ES2926869T3 (OSRAM)
FI (1) FIC20240035I1 (OSRAM)
FR (1) FR24C1039I2 (OSRAM)
HR (2) HRP20201078T1 (OSRAM)
HU (3) HUE050704T2 (OSRAM)
IL (2) IL247714B (OSRAM)
LT (3) LT3757214T (OSRAM)
MX (2) MX373908B (OSRAM)
MY (2) MY192634A (OSRAM)
NL (1) NL301293I2 (OSRAM)
NZ (1) NZ724100A (OSRAM)
PL (2) PL3757214T3 (OSRAM)
PT (2) PT3126499T (OSRAM)
RS (2) RS63487B1 (OSRAM)
RU (1) RU2704619C2 (OSRAM)
SG (3) SG10201910844SA (OSRAM)
SI (2) SI3126499T1 (OSRAM)
SM (2) SMT202000456T1 (OSRAM)
WO (1) WO2015153800A2 (OSRAM)

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KR20210153632A (ko) * 2019-03-26 2021-12-17 루트거스, 더 스테이트 유니버시티 오브 뉴 저지 신경변성 장애를 치료하기 위한 조성물 및 방법
KR20220027059A (ko) * 2019-05-01 2022-03-07 블랙 스완 파마슈티컬스, 인코포레이티드 Sod1 관련 질환의 치료
US11629347B2 (en) 2019-05-06 2023-04-18 University Of Massachusetts Anti-C9ORF72 oligonucleotides and related methods
KR20220007104A (ko) 2019-05-08 2022-01-18 바이오젠 엠에이 인코포레이티드 올리고뉴클레오타이드의 수렴형 액상 합성
PL3976791T3 (pl) * 2019-05-28 2025-08-04 Ionis Pharmaceuticals, Inc. Związki i sposoby do zmniejszania ekspresji fus
WO2022174000A2 (en) 2021-02-12 2022-08-18 Alnylam Pharmaceuticals, Inc. Superoxide dismutase 1 (sod1) irna compositions and methods of use thereof for treating or preventing superoxide dismutase 1- (sod1-) associated neurodegenerative diseases
CA3214585A1 (en) 2021-03-31 2022-10-06 Biogen Ma Inc. Treatment of amyotrophic lateral sclerosis
TW202304473A (zh) 2021-04-01 2023-02-01 美商百健Ma公司 向中樞神經系統之核酸遞送
EP4430191A2 (en) * 2021-11-08 2024-09-18 University Of Massachusetts Oligonucleotides for sod1 modulation
CN114369130B (zh) * 2021-12-28 2023-10-03 杭州天龙药业有限公司 修饰的硫代寡核苷酸及其应用
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