JP2016521995A5 - - Google Patents

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JP2016521995A5
JP2016521995A5 JP2016521453A JP2016521453A JP2016521995A5 JP 2016521995 A5 JP2016521995 A5 JP 2016521995A5 JP 2016521453 A JP2016521453 A JP 2016521453A JP 2016521453 A JP2016521453 A JP 2016521453A JP 2016521995 A5 JP2016521995 A5 JP 2016521995A5
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JP
Japan
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sequence
tracr
target
composition
crispr
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JP2016521453A
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Japanese (ja)
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JP6702858B2 (ja
JP2016521995A (ja
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Priority claimed from PCT/US2013/074667 external-priority patent/WO2014093622A2/en
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Priority claimed from PCT/US2014/041809 external-priority patent/WO2014204729A1/en
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JP2016521453A 2013-06-17 2014-06-11 ウイルス成分を使用して障害および疾患をターゲティングするためのＣＲＩＳＰＲ−Ｃａｓ系および組成物の送達、使用および治療上の適用 Active JP6702858B2 (ja)

Applications Claiming Priority (15)

Application Number Priority Date Filing Date Title
US201361836123P 2013-06-17 2013-06-17
US61/836,123 2013-06-17
US201361847537P 2013-07-17 2013-07-17
US61/847,537 2013-07-17
US201361862355P 2013-08-05 2013-08-05
US61/862,355 2013-08-05
US201361871301P 2013-08-28 2013-08-28
US61/871,301 2013-08-28
US201361915225P 2013-12-12 2013-12-12
PCT/US2013/074667 WO2014093622A2 (en) 2012-12-12 2013-12-12 Delivery, engineering and optimization of systems, methods and compositions for sequence manipulation and therapeutic applications
US61/915,225 2013-12-12
USPCT/US2013/074667 2013-12-12
US201461979879P 2014-04-15 2014-04-15
US61/979,879 2014-04-15
PCT/US2014/041809 WO2014204729A1 (en) 2013-06-17 2014-06-11 Delivery, use and therapeutic applications of the crispr-cas systems and compositions for targeting disorders and diseases using viral components

Publications (3)

Publication Number Publication Date
JP2016521995A JP2016521995A (ja) 2016-07-28
JP2016521995A5 true JP2016521995A5 (Direct) 2017-07-20
JP6702858B2 JP6702858B2 (ja) 2020-06-03

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JP2016521453A Active JP6702858B2 (ja) 2013-06-17 2014-06-11 ウイルス成分を使用して障害および疾患をターゲティングするためのＣＲＩＳＰＲ−Ｃａｓ系および組成物の送達、使用および治療上の適用

Country Status (14)

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US (2) US10946108B2 (Direct)
EP (2) EP3011034B1 (Direct)
JP (1) JP6702858B2 (Direct)
KR (2) KR20160056869A (Direct)
CN (2) CN105793425B (Direct)
AU (1) AU2014281031B2 (Direct)
BR (1) BR122021009076B1 (Direct)
CA (1) CA2915795C (Direct)
IL (1) IL243195B (Direct)
MX (1) MX374532B (Direct)
RU (1) RU2716421C2 (Direct)
SG (2) SG11201510286QA (Direct)
WO (1) WO2014204729A1 (Direct)
ZA (1) ZA201508961B (Direct)

Cited By (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US11591581B2 (en) 2013-12-12 2023-02-28 The Broad Institute, Inc. Compositions and methods of use of CRISPR-Cas systems in nucleotide repeat disorders

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