CN111511375A - 用于基因治疗的腺相关病毒载体 - Google Patents

用于基因治疗的腺相关病毒载体 Download PDF

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Publication number
CN111511375A
CN111511375A CN201880056905.7A CN201880056905A CN111511375A CN 111511375 A CN111511375 A CN 111511375A CN 201880056905 A CN201880056905 A CN 201880056905A CN 111511375 A CN111511375 A CN 111511375A
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aav
mutation
nucleic acid
cells
sequence
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托马斯·亨利
马维斯·阿格班德耶-麦肯纳
蒂尔曼·布尔克斯图默尔
莉蒂亚·维尼
莫达希尔·乔杜里
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Intima Bioscience Inc
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CN201880056905.7A 2017-06-30 2018-06-29 用于基因治疗的腺相关病毒载体 Pending CN111511375A (zh)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201762527937P 2017-06-30 2017-06-30
US62/527,937 2017-06-30
US201862659472P 2018-04-18 2018-04-18
US62/659,472 2018-04-18
US201862665256P 2018-05-01 2018-05-01
US62/665,256 2018-05-01
PCT/US2018/040480 WO2019006418A2 (en) 2017-06-30 2018-06-29 ADENO-ASSOCIATED VIRAL VECTORS FOR GENE THERAPY

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CN111511375A true CN111511375A (zh) 2020-08-07

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US (3) US11098325B2 (https=)
EP (1) EP3645021A4 (https=)
JP (1) JP2020530307A (https=)
CN (1) CN111511375A (https=)
WO (1) WO2019006418A2 (https=)

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CN107002095A (zh) * 2014-05-14 2017-08-01 埃斯蒂维实验室股份有限公司 用于治疗溶酶体贮积症的腺伴随病毒载体
CN113563430A (zh) * 2021-07-30 2021-10-29 上海信致医药科技有限公司 用于治疗眼部疾病的基因递送系统及其应用
CN114276419A (zh) * 2021-12-30 2022-04-05 上海勉亦生物科技有限公司 肌肉高亲和性的新型腺相关病毒衣壳蛋白及其应用
CN114516901A (zh) * 2022-03-11 2022-05-20 上海勉亦生物科技有限公司 一种神经系统高亲和性的aav载体及其应用
CN116287263A (zh) * 2023-03-02 2023-06-23 圣湘生物科技股份有限公司 一种用于甲状腺结节检测的组合物及试剂盒
CN116549667A (zh) * 2023-05-29 2023-08-08 四川普锐特药业有限公司 一种pas修饰的脂质纳米粒、包含其的药物制剂,及其制备方法和用途
CN116693633A (zh) * 2023-02-21 2023-09-05 广州派真生物技术有限公司 腺相关病毒突变体及其应用
CN118480096A (zh) * 2023-09-20 2024-08-13 广州派真生物技术有限公司 腺相关病毒突变体及其应用

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