CN109563509B - 靶向长非编码rna的减小尺寸的自递送核酸化合物 - Google Patents

靶向长非编码rna的减小尺寸的自递送核酸化合物 Download PDF

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CN109563509B
CN109563509B CN201680074348.2A CN201680074348A CN109563509B CN 109563509 B CN109563509 B CN 109563509B CN 201680074348 A CN201680074348 A CN 201680074348A CN 109563509 B CN109563509 B CN 109563509B
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nucleic acid
acid molecule
cell
modified
methyl
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CN109563509A (zh
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乔克·黑德维希·万德松佩勒
格特·万皮尔
詹姆斯·卡迪亚
卡伦·G·布洛克
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Biogazelle NV
Phio Pharmaceuticals Corp
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RXi Pharmaceuticals Corp
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CN201680074348.2A 2015-10-19 2016-10-19 靶向长非编码rna的减小尺寸的自递送核酸化合物 Expired - Fee Related CN109563509B (zh)

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US201562243565P 2015-10-19 2015-10-19
US62/243,565 2015-10-19
PCT/US2016/057608 WO2017070151A1 (en) 2015-10-19 2016-10-19 Reduced size self-delivering nucleic acid compounds targeting long non-coding rna

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CN109563509B true CN109563509B (zh) 2022-08-09

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US (1) US11021707B2 (enExample)
EP (1) EP3365446A4 (enExample)
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CA (1) CA3002744A1 (enExample)
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CN106074591B (zh) 2010-03-24 2020-01-14 菲奥医药公司 眼部症候中的rna干扰
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