JP6954890B2 - ヌクレアーゼ媒介ゲノム遺伝子操作のための送達方法及び組成物 - Google Patents

ヌクレアーゼ媒介ゲノム遺伝子操作のための送達方法及び組成物 Download PDF

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JP6954890B2
JP6954890B2 JP2018501179A JP2018501179A JP6954890B2 JP 6954890 B2 JP6954890 B2 JP 6954890B2 JP 2018501179 A JP2018501179 A JP 2018501179A JP 2018501179 A JP2018501179 A JP 2018501179A JP 6954890 B2 JP6954890 B2 JP 6954890B2
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cells
cell
gene
nuclease
donor
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JP2018525979A5 (Direct
JP2018525979A (ja
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ゲイリー ケー． リー，
ゲイリー ケー． リー，
ブリジット イー． レイリー，
ブリジット イー． レイリー，
マーティン， スーザン ジェイ． セント
マーティン， スーザン ジェイ． セント
トーマス ウェクスラー，
トーマス ウェクスラー，
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Sangamo Therapeutics Inc
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JP2018501179A 2015-07-13 2016-07-13 ヌクレアーゼ媒介ゲノム遺伝子操作のための送達方法及び組成物 Active JP6954890B2 (ja)

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US201562191918P 2015-07-13 2015-07-13
US62/191,918 2015-07-13
US201562247469P 2015-10-28 2015-10-28
US62/247,469 2015-10-28
US201662315438P 2016-03-30 2016-03-30
US62/315,438 2016-03-30
PCT/US2016/042024 WO2017011519A1 (en) 2015-07-13 2016-07-13 Delivery methods and compositions for nuclease-mediated genome engineering

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US (2) US10450585B2 (Direct)
EP (1) EP3322297B1 (Direct)
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CN (1) CN108024544B (Direct)
AU (1) AU2016291778B2 (Direct)
CA (1) CA2991301A1 (Direct)
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AU2016291778B2 (en) 2021-05-06
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EP3322297A1 (en) 2018-05-23
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WO2017011519A1 (en) 2017-01-19
JP2021045166A (ja) 2021-03-25
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