JP6867945B2 - 核内遺伝子出力の標的とされた増強 - Google Patents

核内遺伝子出力の標的とされた増強 Download PDF

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JP6867945B2
JP6867945B2 JP2017518228A JP2017518228A JP6867945B2 JP 6867945 B2 JP6867945 B2 JP 6867945B2 JP 2017518228 A JP2017518228 A JP 2017518228A JP 2017518228 A JP2017518228 A JP 2017518228A JP 6867945 B2 JP6867945 B2 JP 6867945B2
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aso
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クライナー，エイドリアン
アズナレズ，イザベル
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コールド スプリング ハーバー ラボラトリー
コールド スプリング ハーバー ラボラトリー
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JP2017518228A 2014-10-03 2015-10-03 核内遺伝子出力の標的とされた増強 Active JP6867945B2 (ja)

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US201462059847P 2014-10-03 2014-10-03
US62/059,847 2014-10-03
PCT/US2015/053896 WO2016054615A2 (en) 2014-10-03 2015-10-03 Targeted augmentation of nuclear gene output

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CN107109411B (zh) 2014-10-03 2022-07-01 冷泉港实验室 核基因输出的定向增加
US10525076B2 (en) 2015-02-20 2020-01-07 Rosalind Franklin University Of Medicine And Science Antisense compounds targeting genes associated with cystic fibrosis
US9840709B2 (en) 2015-02-20 2017-12-12 Rosalind Franklin University Of Medicine And Science Antisense compounds targeting genes associated with cystic fibrosis
KR102422625B1 (ko) 2015-10-09 2022-07-20 유니버시티 오브 사우스앰톤 유전자 발현의 조절 및 탈조절된 단백질 발현의 스크리닝
KR102604132B1 (ko) 2015-12-14 2023-11-17 콜드스프링하버러보러토리 상염색체 우성 정신 지체 5 및 드라베 증후군의 치료를 위한 안티센스 올리고머
EP3390635A4 (en) * 2015-12-14 2019-05-01 Cold Spring Harbor Laboratory Antisense oligomers for the treatment of a tuberous sclerosis complex
WO2017106292A1 (en) * 2015-12-14 2017-06-22 Cold Spring Harbor Laboratory Compositions and methods for treatment of kidney diseases
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