JP6591956B2 - Ｍｐｓ１を治療するための組成物および方法 - Google Patents

Ｍｐｓ１を治療するための組成物および方法 Download PDF

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JP6591956B2
JP6591956B2 JP2016501864A JP2016501864A JP6591956B2 JP 6591956 B2 JP6591956 B2 JP 6591956B2 JP 2016501864 A JP2016501864 A JP 2016501864A JP 2016501864 A JP2016501864 A JP 2016501864A JP 6591956 B2 JP6591956 B2 JP 6591956B2
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ウイルソン，ジエームズ・エム
ガーダ，ブリトニー・エル
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ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア
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    • C12N9/24—Hydrolases (3) acting on glycosyl compounds (3.2)
    • C12N9/2402—Hydrolases (3) acting on glycosyl compounds (3.2) hydrolysing O- and S- glycosyl compounds (3.2.1)
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    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
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    • C12Y302/01—Glycosidases, i.e. enzymes hydrolysing O- and S-glycosyl compounds (3.2.1)
    • C12Y302/01076—L-Iduronidase (3.2.1.76)

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JP2016501864A 2013-03-15 2014-03-13 Ｍｐｓ１を治療するための組成物および方法 Active JP6591956B2 (ja)

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US201361788724P 2013-03-15 2013-03-15
US61/788,724 2013-03-15
PCT/US2014/025509 WO2014151341A1 (en) 2013-03-15 2014-03-13 Compositions and methods for treating mpsi

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JP2016512683A5 JP2016512683A5 (enExample) 2017-04-13
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JP2016501864A Active JP6591956B2 (ja) 2013-03-15 2014-03-13 Ｍｐｓ１を治療するための組成物および方法
JP2019079881A Pending JP2019134717A (ja) 2013-03-15 2019-04-19 Ｍｐｓ１を治療するための組成物および方法
JP2020148103A Active JP7168621B2 (ja) 2013-03-15 2020-09-03 Ｍｐｓ１を治療するための組成物および方法
JP2022172314A Active JP7553527B2 (ja) 2013-03-15 2022-10-27 Ｍｐｓ１を治療するための組成物および方法

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JP2020148103A Active JP7168621B2 (ja) 2013-03-15 2020-09-03 Ｍｐｓ１を治療するための組成物および方法
JP2022172314A Active JP7553527B2 (ja) 2013-03-15 2022-10-27 Ｍｐｓ１を治療するための組成物および方法

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EP (2) EP2984166B1 (enExample)
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KR (2) KR102346455B1 (enExample)
CN (1) CN105026554B (enExample)
AU (2) AU2014235096B2 (enExample)
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Cited By (1)

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JP2019134717A (ja) * 2013-03-15 2019-08-15 ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア Ｍｐｓ１を治療するための組成物および方法

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