AU2014235096B2 - Compositions and methods for treating MPSI - Google Patents
Compositions and methods for treating MPSI Download PDFInfo
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- AU2014235096B2 AU2014235096B2 AU2014235096A AU2014235096A AU2014235096B2 AU 2014235096 B2 AU2014235096 B2 AU 2014235096B2 AU 2014235096 A AU2014235096 A AU 2014235096A AU 2014235096 A AU2014235096 A AU 2014235096A AU 2014235096 B2 AU2014235096 B2 AU 2014235096B2
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| MX2018007080A (es) * | 2015-12-11 | 2018-11-12 | Univ Pennsylvania | Terapia genica para tratar hipercolesterolemia familiar. |
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| AU2017250298B2 (en) | 2016-04-15 | 2024-10-03 | The Trustees Of The University Of Pennsylvania | Gene therapy for treating mucopolysaccharidosis type II |
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| WO2025035143A1 (en) | 2023-08-10 | 2025-02-13 | The Trustees Of The University Of Pennsylvania | Compositions and methods for treatment of spinal muscular atrophy |
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