JP2021512871A5 - - Google Patents

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Publication number
JP2021512871A5
JP2021512871A5 JP2020541887A JP2020541887A JP2021512871A5 JP 2021512871 A5 JP2021512871 A5 JP 2021512871A5 JP 2020541887 A JP2020541887 A JP 2020541887A JP 2020541887 A JP2020541887 A JP 2020541887A JP 2021512871 A5 JP2021512871 A5 JP 2021512871A5
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Japan
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amino acid
seq
capsid protein
protein corresponding
sequence
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Ceased
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JP2020541887A
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English (en)
Japanese (ja)
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JP2021512871A (ja
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Priority claimed from PCT/US2019/016354 external-priority patent/WO2019152843A1/en
Publication of JP2021512871A publication Critical patent/JP2021512871A/ja
Publication of JP2021512871A5 publication Critical patent/JP2021512871A5/ja
Ceased legal-status Critical Current

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JP2020541887A 2018-02-01 2019-02-01 Pah遺伝子機能を回復させるためのアデノ随伴ウイルス組成物及びそれらの使用方法 Ceased JP2021512871A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201862625149P 2018-02-01 2018-02-01
US62/625,149 2018-02-01
US201862672377P 2018-05-16 2018-05-16
US62/672,377 2018-05-16
PCT/US2019/016354 WO2019152843A1 (en) 2018-02-01 2019-02-01 Adeno-associated virus compositions for restoring pah gene function and methods of use thereof

Publications (2)

Publication Number Publication Date
JP2021512871A JP2021512871A (ja) 2021-05-20
JP2021512871A5 true JP2021512871A5 (OSRAM) 2022-02-09

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JP2020541887A Ceased JP2021512871A (ja) 2018-02-01 2019-02-01 Pah遺伝子機能を回復させるためのアデノ随伴ウイルス組成物及びそれらの使用方法

Country Status (14)

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US (3) US20190256867A1 (OSRAM)
EP (1) EP3746101A4 (OSRAM)
JP (1) JP2021512871A (OSRAM)
KR (1) KR20200127170A (OSRAM)
CN (1) CN111902164A (OSRAM)
AU (1) AU2019215152A1 (OSRAM)
BR (1) BR112020015798A2 (OSRAM)
CA (1) CA3090226A1 (OSRAM)
CL (1) CL2020002008A1 (OSRAM)
CO (1) CO2020010793A2 (OSRAM)
IL (1) IL276368A (OSRAM)
MX (1) MX2020008133A (OSRAM)
PE (1) PE20212076A1 (OSRAM)
WO (1) WO2019152843A1 (OSRAM)

Families Citing this family (5)

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MX2022008677A (es) * 2020-01-16 2022-08-10 Takeda Pharmaceuticals Co Terapia genica basada en virus adenoasociados para la fenilcetonuria.
US20210361778A1 (en) * 2020-04-06 2021-11-25 Homology Medicines, Inc. Adeno-associated virus compositions for ids gene transfer and methods of use thereof
TW202208632A (zh) * 2020-05-27 2022-03-01 美商同源醫藥公司 用於恢復pah基因功能的腺相關病毒組成物及其使用方法
US12173308B2 (en) 2020-10-01 2024-12-24 Genzyme Corporation Human PAH expression cassette for treatment of PKU by liver-directed gene replacement therapy

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