AU2019215152A1 - Adeno-associated virus compositions for restoring PAH gene function and methods of use thereof - Google Patents
Adeno-associated virus compositions for restoring PAH gene function and methods of use thereof Download PDFInfo
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- AU2019215152A1 AU2019215152A1 AU2019215152A AU2019215152A AU2019215152A1 AU 2019215152 A1 AU2019215152 A1 AU 2019215152A1 AU 2019215152 A AU2019215152 A AU 2019215152A AU 2019215152 A AU2019215152 A AU 2019215152A AU 2019215152 A1 AU2019215152 A1 AU 2019215152A1
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- amino acid
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- capsid protein
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| PCT/US2019/016354 WO2019152843A1 (en) | 2018-02-01 | 2019-02-01 | Adeno-associated virus compositions for restoring pah gene function and methods of use thereof |
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| MX2022008677A (es) * | 2020-01-16 | 2022-08-10 | Takeda Pharmaceuticals Co | Terapia genica basada en virus adenoasociados para la fenilcetonuria. |
| US20210361778A1 (en) * | 2020-04-06 | 2021-11-25 | Homology Medicines, Inc. | Adeno-associated virus compositions for ids gene transfer and methods of use thereof |
| TW202208632A (zh) * | 2020-05-27 | 2022-03-01 | 美商同源醫藥公司 | 用於恢復ｐａｈ基因功能的腺相關病毒組成物及其使用方法 |
| US12173308B2 (en) | 2020-10-01 | 2024-12-24 | Genzyme Corporation | Human PAH expression cassette for treatment of PKU by liver-directed gene replacement therapy |
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| MX2020008133A (es) | 2020-10-14 |
| JP2021512871A (ja) | 2021-05-20 |
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| US20220325302A1 (en) | 2022-10-13 |
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| EP3746101A1 (en) | 2020-12-09 |
| PE20212076A1 (es) | 2021-10-26 |
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| US20210130794A1 (en) | 2021-05-06 |
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| WO2019152843A1 (en) | 2019-08-08 |
| IL276368A (en) | 2020-09-30 |
| CL2020002008A1 (es) | 2021-02-12 |
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