JP2021513871A5 - - Google Patents

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Publication number
JP2021513871A5
JP2021513871A5 JP2020566527A JP2020566527A JP2021513871A5 JP 2021513871 A5 JP2021513871 A5 JP 2021513871A5 JP 2020566527 A JP2020566527 A JP 2020566527A JP 2020566527 A JP2020566527 A JP 2020566527A JP 2021513871 A5 JP2021513871 A5 JP 2021513871A5
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amino acid
seq
capsid protein
protein corresponding
aav
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JP2020566527A
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JP7244547B2 (ja
JP2021513871A (ja
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Priority claimed from PCT/US2019/018502 external-priority patent/WO2019161365A1/en
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JP2020566527A 2018-02-19 2019-02-19 Ｆ８遺伝子機能を回復させるためのアデノ随伴ウイルス組成物及びその使用の方法 Active JP7244547B2 (ja)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201862632300P 2018-02-19 2018-02-19
US62/632,300 2018-02-19
US201862632919P 2018-02-20 2018-02-20
US62/632,919 2018-02-20
US201862672385P 2018-05-16 2018-05-16
US62/672,385 2018-05-16
PCT/US2019/018502 WO2019161365A1 (en) 2018-02-19 2019-02-19 Adeno-associated virus compositions for restoring f8 gene function and methods of use thereof

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JP2021513871A JP2021513871A (ja) 2021-06-03
JP2021513871A5 true JP2021513871A5 (OSRAM) 2022-03-02
JP7244547B2 JP7244547B2 (ja) 2023-03-22

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US (2) US11306329B2 (OSRAM)
EP (1) EP3755795A4 (OSRAM)
JP (1) JP7244547B2 (OSRAM)
CN (1) CN112041437A (OSRAM)
WO (1) WO2019161365A1 (OSRAM)

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US20250101465A1 (en) * 2021-05-11 2025-03-27 City Of Hope Adeno-associated virus compositions and methods of use thereof
WO2024229281A1 (en) * 2023-05-02 2024-11-07 City Of Hope Adeno-associated virus compositions and methods of use thereof

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EP3562514B1 (en) 2016-12-30 2026-04-29 The Trustees Of The University Of Pennsylvania Gene therapy for treating wilson's disease
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