CN116096734A - Aav衣壳的向性的重定向 - Google Patents

Aav衣壳的向性的重定向 Download PDF

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Publication number
CN116096734A
CN116096734A CN202180049682.3A CN202180049682A CN116096734A CN 116096734 A CN116096734 A CN 116096734A CN 202180049682 A CN202180049682 A CN 202180049682A CN 116096734 A CN116096734 A CN 116096734A
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seq
amino acid
acid sequence
aav capsid
aav
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Pending
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CN202180049682.3A
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Chinese (zh)
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M·E·农嫩马赫
侯金兆
W·王
M·蔡尔德
S·李
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Voyager Therapeutics Inc
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Voyager Therapeutics Inc
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    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
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CN202180049682.3A 2020-05-13 2021-03-31 Aav衣壳的向性的重定向 Pending CN116096734A (zh)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202063023927P 2020-05-13 2020-05-13
US63/023,927 2020-05-13
US202063122300P 2020-12-07 2020-12-07
US63/122,300 2020-12-07
PCT/US2021/025061 WO2021230987A1 (en) 2020-05-13 2021-03-31 Redirection of tropism of aav capsids

Publications (1)

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CN116096734A true CN116096734A (zh) 2023-05-09

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US (3) US20230203102A1 (https=)
EP (1) EP4149955A1 (https=)
JP (2) JP7731909B2 (https=)
KR (1) KR20230022175A (https=)
CN (1) CN116096734A (https=)
AU (1) AU2021273447B2 (https=)
BR (1) BR112022023106A2 (https=)
CA (1) CA3182970A1 (https=)
CO (1) CO2022016156A2 (https=)
IL (1) IL298001A (https=)
MX (1) MX2022014256A (https=)
PE (1) PE20230767A1 (https=)
TW (1) TWI900553B (https=)
WO (1) WO2021230987A1 (https=)

Cited By (2)

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CN113316639A (zh) * 2018-11-16 2021-08-27 阿斯克肋匹奥生物制药公司 用于治疗庞贝氏病的治疗性腺相关病毒
CN118324853A (zh) * 2024-04-03 2024-07-12 广州派真生物技术有限公司 腺相关病毒突变体及其应用

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