CN107980062B - 用于靶向亨廷汀mRNA的寡核苷酸化合物 - Google Patents

用于靶向亨廷汀mRNA的寡核苷酸化合物 Download PDF

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CN107980062B
CN107980062B CN201680031524.4A CN201680031524A CN107980062B CN 107980062 B CN107980062 B CN 107980062B CN 201680031524 A CN201680031524 A CN 201680031524A CN 107980062 B CN107980062 B CN 107980062B
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nucleotides
rna
target
mrna
gene
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CN107980062A (zh
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阿纳斯塔西娅·科威罗娃
尼尔·阿罗宁
茱莉亚·奥尔特曼
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University of Massachusetts Amherst
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CN201680031524.4A 2015-04-03 2016-04-01 用于靶向亨廷汀mRNA的寡核苷酸化合物 Active CN107980062B (zh)

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US201562142731P 2015-04-03 2015-04-03
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US201662289274P 2016-01-31 2016-01-31
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PCT/US2016/025722 WO2016161374A1 (en) 2015-04-03 2016-04-01 Oligonucleotide compounds for targeting huntingtin mrna

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