AU2018309187C1 - Methods and compositions for modulating splicing - Google Patents

Methods and compositions for modulating splicing Download PDF

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AU2018309187C1
AU2018309187C1 AU2018309187A AU2018309187A AU2018309187C1 AU 2018309187 C1 AU2018309187 C1 AU 2018309187C1 AU 2018309187 A AU2018309187 A AU 2018309187A AU 2018309187 A AU2018309187 A AU 2018309187A AU 2018309187 C1 AU2018309187 C1 AU 2018309187C1
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substituted
unsubstituted
alkyl
ring
heteroaryl
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AU2018309187B2 (en
AU2018309187A1 (en
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William Haney
Michael Luzzio
Kathleen Mccarthy
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Skyhawk Therapeutics Inc
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Skyhawk Therapeutics Inc
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AU2018309187A 2017-08-04 2018-08-03 Methods and compositions for modulating splicing Active AU2018309187C1 (en)

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US201762541202P 2017-08-04 2017-08-04
US62/541,202 2017-08-04
US201762562927P 2017-09-25 2017-09-25
US201762562948P 2017-09-25 2017-09-25
US62/562,948 2017-09-25
US62/562,927 2017-09-25
PCT/US2018/045282 WO2019028440A1 (en) 2017-08-04 2018-08-03 METHODS AND COMPOSITIONS FOR MODULATING SPLICING

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CN108697709A (zh) 2015-12-10 2018-10-23 Ptc医疗公司 用于治疗亨廷顿病的方法
AU2017363369A1 (en) 2016-11-28 2019-05-30 Ptc Therapeutics, Inc Methods for modulating RNA splicing
AU2018282154B2 (en) 2017-06-05 2022-04-07 Ptc Therapeutics, Inc. Compounds for treating huntington's disease
US11608501B2 (en) 2017-06-14 2023-03-21 Ptc Therapeutics, Inc. Methods for modifying RNA splicing
CN111182898B (zh) 2017-06-28 2024-04-16 Ptc医疗公司 用于治疗亨廷顿氏病的方法
WO2019005993A1 (en) 2017-06-28 2019-01-03 Ptc Therapeutics, Inc. METHODS OF TREATING HUNTINGTON'S DISEASE
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