TWI689587B - 用於杜顯氏肌肉萎縮症(dmd)之多重外顯子跳躍組合物 - Google Patents

用於杜顯氏肌肉萎縮症(dmd)之多重外顯子跳躍組合物 Download PDF

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TWI689587B
TWI689587B TW107120221A TW107120221A TWI689587B TW I689587 B TWI689587 B TW I689587B TW 107120221 A TW107120221 A TW 107120221A TW 107120221 A TW107120221 A TW 107120221A TW I689587 B TWI689587 B TW I689587B
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seq
exon
antisense oligonucleotide
antisense
subunit
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TW107120221A
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TW201831687A (zh
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賽薩尼彼得
科爾瑞塞德
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美商薩羅塔治療公司
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TW107120221A 2008-10-24 2009-10-26 用於杜顯氏肌肉萎縮症(dmd)之多重外顯子跳躍組合物 TWI689587B (zh)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US10841608P 2008-10-24 2008-10-24
US61/108,416 2008-10-24
WOPCT/US09/61960 2009-10-23
US12/605,276 US8871918B2 (en) 2008-10-24 2009-10-23 Multiple exon skipping compositions for DMD
US12/605,276 2009-10-23
??PCT/US09/61960 2009-10-23
PCT/US2009/061960 WO2010048586A1 (en) 2008-10-24 2009-10-23 Multiple exon skipping compositions for dmd

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TW201831687A TW201831687A (zh) 2018-09-01
TWI689587B true TWI689587B (zh) 2020-04-01

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TW107120221A TWI689587B (zh) 2008-10-24 2009-10-26 用於杜顯氏肌肉萎縮症(dmd)之多重外顯子跳躍組合物
TW111117662A TW202309285A (zh) 2008-10-24 2009-10-26 用於杜顯氏肌肉萎縮症(dmd)之多重外顯子跳躍組合物
TW098136375A TWI488965B (zh) 2008-10-24 2009-10-26 用於杜顯氏肌肉萎縮症（ｄｍｄ）之多重外顯子跳躍組合物
TW103141650A TWI563086B (en) 2008-10-24 2009-10-26 Multiple exon skipping compositions for dmd
TW113110982A TW202500744A (zh) 2008-10-24 2009-10-26 用於杜顯氏肌肉萎縮症(dmd)之多重外顯子跳躍組合物
TW109105707A TW202043473A (zh) 2008-10-24 2009-10-26 用於杜顯氏肌肉萎縮症(dmd)之多重外顯子跳躍組合物
TW105129379A TWI639700B (zh) 2008-10-24 2009-10-26 用於杜顯氏肌肉萎縮症（ｄｍｄ）之多重外顯子跳躍組合物

Family Applications After (6)

Application Number Title Priority Date Filing Date
TW111117662A TW202309285A (zh) 2008-10-24 2009-10-26 用於杜顯氏肌肉萎縮症(dmd)之多重外顯子跳躍組合物
TW098136375A TWI488965B (zh) 2008-10-24 2009-10-26 用於杜顯氏肌肉萎縮症（ｄｍｄ）之多重外顯子跳躍組合物
TW103141650A TWI563086B (en) 2008-10-24 2009-10-26 Multiple exon skipping compositions for dmd
TW113110982A TW202500744A (zh) 2008-10-24 2009-10-26 用於杜顯氏肌肉萎縮症(dmd)之多重外顯子跳躍組合物
TW109105707A TW202043473A (zh) 2008-10-24 2009-10-26 用於杜顯氏肌肉萎縮症(dmd)之多重外顯子跳躍組合物
TW105129379A TWI639700B (zh) 2008-10-24 2009-10-26 用於杜顯氏肌肉萎縮症（ｄｍｄ）之多重外顯子跳躍組合物

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US (15) US8871918B2 (enExample)
EP (7) EP3133160B1 (enExample)
JP (10) JP5864257B2 (enExample)
KR (6) KR20230025924A (enExample)
CN (4) CN112574988A (enExample)
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BR (3) BRPI0920276B1 (enExample)
CA (2) CA3066050A1 (enExample)
CY (1) CY1122369T1 (enExample)
DK (1) DK3133160T3 (enExample)
ES (2) ES2955539T3 (enExample)
HR (1) HRP20190387T1 (enExample)
HU (1) HUE042979T2 (enExample)
IL (6) IL313162A (enExample)
LT (1) LT3133160T (enExample)
PL (1) PL3133160T3 (enExample)
PT (1) PT3133160T (enExample)
SI (1) SI3133160T1 (enExample)
SM (1) SMT201900159T1 (enExample)
TR (1) TR201902952T4 (enExample)
TW (7) TWI689587B (enExample)
WO (1) WO2010048586A1 (enExample)

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