RU2683497C2 - Композиция и способы высокоэффективного переноса генов с помощью вариантов капсида aav - Google Patents

Композиция и способы высокоэффективного переноса генов с помощью вариантов капсида aav Download PDF

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RU2683497C2
RU2683497C2 RU2014146159A RU2014146159A RU2683497C2 RU 2683497 C2 RU2683497 C2 RU 2683497C2 RU 2014146159 A RU2014146159 A RU 2014146159A RU 2014146159 A RU2014146159 A RU 2014146159A RU 2683497 C2 RU2683497 C2 RU 2683497C2
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nucleic acid
aav
acid sequence
heterologous nucleic
vector
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RU2014146159A (ru
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Мустафа Н. ЯЗИСИОГЛУ
Федерико МИНГОЗЗИ
Хавьер АНГЕЛА
Кэтрин А. ХАЙ
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Дзе Чилдрен'З Хоспитал Оф Филадельфия
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RU2014146159A 2012-04-18 2013-04-18 Композиция и способы высокоэффективного переноса генов с помощью вариантов капсида aav RU2683497C2 (ru)

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US201261635273P 2012-04-18 2012-04-18
US61/635,273 2012-04-18
US201361794995P 2013-03-15 2013-03-15
US61/794,995 2013-03-15
PCT/US2013/037170 WO2013158879A1 (en) 2012-04-18 2013-04-18 Composition and methods for highly efficient gene transfer using aav capsid variants

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RU2014146159A RU2014146159A (ru) 2016-06-10
RU2683497C2 true RU2683497C2 (ru) 2019-03-28

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