KR20220084437A - 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법 - Google Patents

대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법 Download PDF

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KR20220084437A
KR20220084437A KR1020227019810A KR20227019810A KR20220084437A KR 20220084437 A KR20220084437 A KR 20220084437A KR 1020227019810 A KR1020227019810 A KR 1020227019810A KR 20227019810 A KR20227019810 A KR 20227019810A KR 20220084437 A KR20220084437 A KR 20220084437A
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certain embodiments
dose
antisense
administered
subject
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씨. 프랑크 메네트
젠 훙
프랑크 리고
아드리안 알. 크래이너
이민 후아
마르코 에이. 파시니
럼야 쉬해버딘
성 에이치. 청
캐더린 더블유. 클리거
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바이오젠 엠에이 인코포레이티드
콜드스프링하버러보러토리
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First worldwide family litigation filed litigation Critical https://patents.darts-ip.com/?family=43356760&utm_source=google_patent&utm_medium=platform_link&utm_campaign=public_patent_search&patent=KR20220084437(A) "Global patent litigation dataset” by Darts-ip is licensed under a Creative Commons Attribution 4.0 International License.
Application filed by 바이오젠 엠에이 인코포레이티드, 콜드스프링하버러보러토리 filed Critical 바이오젠 엠에이 인코포레이티드
Priority to KR1020247007557A priority Critical patent/KR20240036132A/ko
Publication of KR20220084437A publication Critical patent/KR20220084437A/ko
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  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
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KR1020227019810A 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법 Ceased KR20220084437A (ko)

Priority Applications (1)

Application Number Priority Date Filing Date Title
KR1020247007557A KR20240036132A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
US21803109P 2009-06-17 2009-06-17
US61/218,031 2009-06-17
KR1020217014192A KR20210057223A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
PCT/US2010/039077 WO2010148249A1 (en) 2009-06-17 2010-06-17 Compositions and methods for modulation of smn2 splicing in a subject

Related Parent Applications (1)

Application Number Title Priority Date Filing Date
KR1020217014192A Division KR20210057223A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법

Related Child Applications (1)

Application Number Title Priority Date Filing Date
KR1020247007557A Division KR20240036132A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법

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KR20220084437A true KR20220084437A (ko) 2022-06-21

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ID=43356760

Family Applications (9)

Application Number Title Priority Date Filing Date
KR1020227019810A Ceased KR20220084437A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
KR1020267002500A Pending KR20260021813A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
KR1020127001244A Ceased KR20120093138A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
KR1020207012412A Ceased KR20200047790A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
KR1020217014192A Ceased KR20210057223A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
KR1020177011876A Withdrawn KR20170054537A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
KR1020247007557A Ceased KR20240036132A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
KR1020197009268A Ceased KR20190037378A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
KR1020197003809A Active KR101965868B1 (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법

Family Applications After (8)

Application Number Title Priority Date Filing Date
KR1020267002500A Pending KR20260021813A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
KR1020127001244A Ceased KR20120093138A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
KR1020207012412A Ceased KR20200047790A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
KR1020217014192A Ceased KR20210057223A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
KR1020177011876A Withdrawn KR20170054537A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
KR1020247007557A Ceased KR20240036132A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
KR1020197009268A Ceased KR20190037378A (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
KR1020197003809A Active KR101965868B1 (ko) 2009-06-17 2010-06-17 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법

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US (5) US8980853B2 (enExample)
EP (4) EP2442816A4 (enExample)
JP (8) JP5707396B2 (enExample)
KR (9) KR20220084437A (enExample)
CN (5) CN106983768B (enExample)
AU (2) AU2010262862C1 (enExample)
CA (1) CA2765396C (enExample)
CY (2) CY1120807T1 (enExample)
DK (2) DK3449926T3 (enExample)
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HK (1) HK1246648B (enExample)
HR (2) HRP20181712T1 (enExample)
HU (2) HUE039741T2 (enExample)
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NZ (2) NZ597071A (enExample)
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PT (2) PT3449926T (enExample)
RU (2) RU2566724C9 (enExample)
SI (2) SI3449926T1 (enExample)
SM (2) SMT202000020T1 (enExample)
TR (1) TR201816256T4 (enExample)
WO (1) WO2010148249A1 (enExample)

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US8067571B2 (en) 2005-07-13 2011-11-29 Avi Biopharma, Inc. Antibacterial antisense oligonucleotide and method
BRPI0923225A2 (pt) 2008-12-02 2016-10-04 Chiralgen Ltd metodo para sintese de acidos nucleicos modificados no atomo de fosforo
KR20220084437A (ko) 2009-06-17 2022-06-21 바이오젠 엠에이 인코포레이티드 대상에게서 ｓｍｎ２ 스플라이싱을 조정하기 위한 조성물 및 방법
EP2451461A4 (en) 2009-07-06 2013-05-29 Ontorii Inc NOVEL NUCLEIC ACID PRODRUGS AND METHOD OF USE THEREOF
US8802642B2 (en) 2010-04-28 2014-08-12 Iowa State University Research Foundation, Inc. Spinal muscular atrophy treatment via targeting SMN2 catalytic core
KR101981705B1 (ko) 2010-05-28 2019-05-24 사렙타 쎄러퓨틱스, 인코퍼레이티드 변형된 서브유니트간 결합 및/또는 말단 그룹을 갖는 올리고뉴클레오타이드 유사체
TWI541024B (zh) 2010-09-01 2016-07-11 日本新藥股份有限公司 反義核酸
WO2012031243A2 (en) 2010-09-03 2012-03-08 Avi Biopharma, Inc. dsRNA MOLECULES COMPRISING OLIGONUCLEOTIDE ANALOGS HAVING MODIFIED INTERSUBUNIT LINKAGES AND/OR TERMINAL GROUPS
DK2620428T3 (da) 2010-09-24 2019-07-01 Wave Life Sciences Ltd Asymmetrisk hjælpegruppe
EP3702460A1 (en) 2010-11-12 2020-09-02 The General Hospital Corporation Polycomb-associated non-coding rnas
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