JPWO2020033899A5 - - Google Patents

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JPWO2020033899A5
JPWO2020033899A5 JP2021507003A JP2021507003A JPWO2020033899A5 JP WO2020033899 A5 JPWO2020033899 A5 JP WO2020033899A5 JP 2021507003 A JP2021507003 A JP 2021507003A JP 2021507003 A JP2021507003 A JP 2021507003A JP WO2020033899 A5 JPWO2020033899 A5 JP WO2020033899A5
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JP
Japan
Prior art keywords
nucleotide
snp
nucleotides
optionally
position nucleotide
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Pending
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JP2021507003A
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English (en)
Japanese (ja)
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JP2021533762A (ja
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Priority claimed from PCT/US2019/046013 external-priority patent/WO2020033899A1/en
Publication of JP2021533762A publication Critical patent/JP2021533762A/ja
Publication of JPWO2020033899A5 publication Critical patent/JPWO2020033899A5/ja
Pending legal-status Critical Current

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JP2021507003A 2018-08-10 2019-08-09 Snpを標的化する修飾オリゴヌクレオチド Pending JP2021533762A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201862717287P 2018-08-10 2018-08-10
US62/717,287 2018-08-10
US201962825429P 2019-03-28 2019-03-28
US62/825,429 2019-03-28
PCT/US2019/046013 WO2020033899A1 (en) 2018-08-10 2019-08-09 Modified oligonucleotides targeting snps

Publications (2)

Publication Number Publication Date
JP2021533762A JP2021533762A (ja) 2021-12-09
JPWO2020033899A5 true JPWO2020033899A5 (ru) 2022-08-18

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ID=69414459

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JP2021507003A Pending JP2021533762A (ja) 2018-08-10 2019-08-09 Snpを標的化する修飾オリゴヌクレオチド

Country Status (12)

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US (2) US11827882B2 (ru)
EP (1) EP3833763A4 (ru)
JP (1) JP2021533762A (ru)
KR (1) KR20210093227A (ru)
CN (1) CN112805383A (ru)
AU (1) AU2019316640A1 (ru)
BR (1) BR112021002440A2 (ru)
CA (1) CA3109133A1 (ru)
IL (1) IL280724A (ru)
MX (1) MX2021001590A (ru)
SG (1) SG11202101288TA (ru)
WO (1) WO2020033899A1 (ru)

Families Citing this family (9)

* Cited by examiner, † Cited by third party
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US20210115442A1 (en) * 2019-08-23 2021-04-22 University Of Massachusetts O-methyl rich fully stabilized oligonucleotides
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KR20230162024A (ko) 2021-03-29 2023-11-28 알닐람 파마슈티칼스 인코포레이티드 헌팅틴(HTT) iRNA 제제 조성물 및 이의 사용 방법
KR20240040729A (ko) 2021-06-23 2024-03-28 유니버시티 오브 매사추세츠 자간전증 및 기타 혈관신생 질환의 치료를 위한 최적화된 항-flt1 올리고뉴클레오타이드 화합물
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