JPWO2020023737A5 - - Google Patents
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- JPWO2020023737A5 JPWO2020023737A5 JP2021503566A JP2021503566A JPWO2020023737A5 JP WO2020023737 A5 JPWO2020023737 A5 JP WO2020023737A5 JP 2021503566 A JP2021503566 A JP 2021503566A JP 2021503566 A JP2021503566 A JP 2021503566A JP WO2020023737 A5 JPWO2020023737 A5 JP WO2020023737A5
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- seq
- nucleobases
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| US20200283800A1 (en) * | 2017-10-23 | 2020-09-10 | Prevail Therapeutics, Inc. | Gene therapies for neurodegenerative diseases |
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| JP2015092853A (ja) | 2013-11-12 | 2015-05-18 | 国立大学法人名古屋大学 | Ａｌｓ疾患関連遺伝子配列解析用の補足ｐｃｒプライマーセット、ａｌｓ疾患関連遺伝子配列の解析方法、及びａｌｓ疾患の検査方法 |
| WO2015143245A1 (en) * | 2014-03-19 | 2015-09-24 | Isis Pharmaceuticals, Inc. | Methods for modulating ataxin 2 expression |
| RS62526B1 (sr) * | 2014-03-19 | 2021-11-30 | Ionis Pharmaceuticals Inc | Kompozicije za modulaciju ekspresije ataksina 2 |
| MA43072A (fr) | 2015-07-22 | 2018-05-30 | Wave Life Sciences Ltd | Compositions d'oligonucléotides et procédés associés |
| EP3397288A4 (en) | 2015-12-31 | 2019-09-11 | Ionis Pharmaceuticals, Inc. | METHODS FOR REDUCING THE EXPRESSION OF ATAXIN-2 |
| JP7411632B2 (ja) | 2018-07-25 | 2024-01-11 | アイオーニス ファーマシューティカルズ， インコーポレーテッド | Ａｔｘｎ２発現を低減するための化合物及び方法 |
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