JP7565218B2 - 筋萎縮性側索硬化症および脊髄に関連する障害の治療 - Google Patents

筋萎縮性側索硬化症および脊髄に関連する障害の治療 Download PDF

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JP7565218B2
JP7565218B2 JP2020570046A JP2020570046A JP7565218B2 JP 7565218 B2 JP7565218 B2 JP 7565218B2 JP 2020570046 A JP2020570046 A JP 2020570046A JP 2020570046 A JP2020570046 A JP 2020570046A JP 7565218 B2 JP7565218 B2 JP 7565218B2
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sequence
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exon
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ウェン－イー サー、ディナー
チェン、チンミン
ソーパー、ジェナ キャロル
パツケ、ホルガー
ホウ、ジンジャオ
エム． ハーシュ、スティーブン
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Voyager Therapeutics Inc
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JP2020570046A 2018-07-02 2019-07-02 筋萎縮性側索硬化症および脊髄に関連する障害の治療 Active JP7565218B2 (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201862693040P 2018-07-02 2018-07-02
US62/693,040 2018-07-02
US201862746104P 2018-10-16 2018-10-16
US62/746,104 2018-10-16
PCT/US2019/040230 WO2020010042A1 (en) 2018-07-02 2019-07-02 Treatment of amyotrophic lateral sclerosis and disorders associated with the spinal cord

Publications (4)

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JP2021529513A JP2021529513A (ja) 2021-11-04
JP2021529513A5 JP2021529513A5 (https=) 2022-07-11
JPWO2020010042A5 JPWO2020010042A5 (https=) 2022-07-11
JP7565218B2 true JP7565218B2 (ja) 2024-10-10

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US (1) US20210254103A1 (https=)
EP (1) EP3818161A1 (https=)
JP (1) JP7565218B2 (https=)
CN (1) CN112567035A (https=)
AU (1) AU2019299861A1 (https=)
CA (1) CA3103963A1 (https=)
WO (1) WO2020010042A1 (https=)

Families Citing this family (10)

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CN119876138A (zh) 2014-11-14 2025-04-25 沃雅戈治疗公司 调节性多核苷酸
CA3193811A1 (en) 2014-11-14 2016-05-19 Voyager Therapeutics, Inc. Compositions and methods of treating amyotrophic lateral sclerosis (als)
CA3024448C (en) 2016-05-18 2025-09-09 Voyager Therapeutics, Inc. MODULATING POLYNUCLEOTIDES
EP3618839A4 (en) 2017-05-05 2021-06-09 Voyager Therapeutics, Inc. COMPOSITIONS AND METHODS OF TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
TW202413649A (zh) 2017-10-16 2024-04-01 美商航海家醫療公司 肌萎縮性脊髓側索硬化症(als)之治療
WO2019079242A1 (en) 2017-10-16 2019-04-25 Voyager Therapeutics, Inc. TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)
WO2020223296A1 (en) * 2019-04-29 2020-11-05 Voyager Therapeutics, Inc. Treatment of amyotrophic lateral sclerosis and disorders associated with the spinal cord
WO2022174000A2 (en) 2021-02-12 2022-08-18 Alnylam Pharmaceuticals, Inc. Superoxide dismutase 1 (sod1) irna compositions and methods of use thereof for treating or preventing superoxide dismutase 1- (sod1-) associated neurodegenerative diseases
WO2024226761A2 (en) 2023-04-26 2024-10-31 Voyager Therapeutics, Inc. Compositions and methods for treating amyotrophic lateral sclerosis
WO2025045130A1 (zh) * 2023-08-29 2025-03-06 石药集团中奇制药技术（石家庄）有限公司 一种抑制sod1基因表达的dsrna分子及其应用

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